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A randomised Phase I/II trial to evaluate the efficacy and safety of orally administered Oxalobacter formigenes to treat primary hyperoxaluria.
Hoppe, Bernd; Niaudet, Patrick; Salomon, Rémi; Harambat, Jérôme; Hulton, Sally-Anne; Van't Hoff, William; Moochhala, Shabbir H; Deschênes, Georges; Lindner, Elisabeth; Sjögren, Anna; Cochat, Pierre.
Afiliação
  • Hoppe B; Department of Pediatrics, Division of Pediatric Nephrology, University Hospital Bonn, Adenauerallee 119, D-53113, Bonn, Germany. bernd.hoppe@ukb.uni-bonn.de.
  • Niaudet P; Pediatric Nephrology, Necker Hospital, Université Paris-Descartes, Paris, France.
  • Salomon R; Pediatric Nephrology, Necker Hospital, Université Paris-Descartes, Paris, France.
  • Harambat J; Centre de référence Maladies Rénales Rares du Sud-Ouest, Centre Hospitalier Universitaire de Bordeaux, Bordeaux, France.
  • Hulton SA; Department of Paediatric Nephrology, Birmingham Children's Hospital NHS Foundation Trust, Birmingham, UK.
  • Van't Hoff W; Renal Unit, Great Ormond Street Hospital, London, UK.
  • Moochhala SH; UCL Centre for Nephrology, Royal Free Campus and Hospital, London, UK.
  • Deschênes G; Pediatric Nephrology Department, Robert Debré Hospital, Paris, France.
  • Lindner E; OxThera AB, Stockholm, Sweden.
  • Sjögren A; OxThera AB, Stockholm, Sweden.
  • Cochat P; Centre de référence des Maladies Rénales Rares, Hôpital Femme Mère Enfant, Bron, France.
Pediatr Nephrol ; 32(5): 781-790, 2017 05.
Article em En | MEDLINE | ID: mdl-27924398

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Hiperoxalúria / Oxalobacter formigenes Tipo de estudo: Clinical_trials Limite: Adolescent / Adult / Child / Child, preschool / Female / Humans / Male Idioma: En Revista: Pediatr Nephrol Assunto da revista: NEFROLOGIA / PEDIATRIA Ano de publicação: 2017 Tipo de documento: Article País de afiliação: Alemanha

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Hiperoxalúria / Oxalobacter formigenes Tipo de estudo: Clinical_trials Limite: Adolescent / Adult / Child / Child, preschool / Female / Humans / Male Idioma: En Revista: Pediatr Nephrol Assunto da revista: NEFROLOGIA / PEDIATRIA Ano de publicação: 2017 Tipo de documento: Article País de afiliação: Alemanha