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LRRK2 Antisense Oligonucleotides Ameliorate α-Synuclein Inclusion Formation in a Parkinson's Disease Mouse Model.
Zhao, Hien Tran; John, Neena; Delic, Vedad; Ikeda-Lee, Karli; Kim, Aneeza; Weihofen, Andreas; Swayze, Eric E; Kordasiewicz, Holly B; West, Andrew B; Volpicelli-Daley, Laura A.
Afiliação
  • Zhao HT; Ionis Pharmaceuticals, Inc., Carlsbad, CA 92010, USA. Electronic address: hzhao@ionisph.com.
  • John N; Center for Neurodegeneration and Experimental Therapeutics, University of Alabama, Birmingham, AL 35294, USA.
  • Delic V; Center for Neurodegeneration and Experimental Therapeutics, University of Alabama, Birmingham, AL 35294, USA.
  • Ikeda-Lee K; Ionis Pharmaceuticals, Inc., Carlsbad, CA 92010, USA.
  • Kim A; Ionis Pharmaceuticals, Inc., Carlsbad, CA 92010, USA.
  • Weihofen A; Biogen, Cambridge, MA 02142, USA.
  • Swayze EE; Ionis Pharmaceuticals, Inc., Carlsbad, CA 92010, USA.
  • Kordasiewicz HB; Ionis Pharmaceuticals, Inc., Carlsbad, CA 92010, USA.
  • West AB; Center for Neurodegeneration and Experimental Therapeutics, University of Alabama, Birmingham, AL 35294, USA.
  • Volpicelli-Daley LA; Center for Neurodegeneration and Experimental Therapeutics, University of Alabama, Birmingham, AL 35294, USA. Electronic address: lvolpicellidaley@uabmc.edu.
Mol Ther Nucleic Acids ; 8: 508-519, 2017 Sep 15.
Article em En | MEDLINE | ID: mdl-28918051

Texto completo: 1 Base de dados: MEDLINE Idioma: En Revista: Mol Ther Nucleic Acids Ano de publicação: 2017 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Idioma: En Revista: Mol Ther Nucleic Acids Ano de publicação: 2017 Tipo de documento: Article