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Asfotase alfa for infants and young children with hypophosphatasia: 7 year outcomes of a single-arm, open-label, phase 2 extension trial.
Whyte, Michael P; Simmons, Jill H; Moseley, Scott; Fujita, Kenji P; Bishop, Nicholas; Salman, Nada J; Taylor, John; Phillips, Dawn; McGinn, Mairead; McAlister, William H.
Afiliação
  • Whyte MP; Center for Metabolic Bone Disease and Molecular Research, Shriners Hospital for Children, St Louis, MO, USA; Division of Bone and Mineral Diseases, Department of Internal Medicine, Washington University School of Medicine at Barnes-Jewish Hospital, St Louis, MO, USA. Electronic address: mwhyte@shrin
  • Simmons JH; Vanderbilt University Medical Center, Department of Pediatrics, Vanderbilt University, Nashville, TN, USA.
  • Moseley S; Alexion Pharmaceuticals, Boston, MA, USA.
  • Fujita KP; Alexion Pharmaceuticals, Boston, MA, USA.
  • Bishop N; Sheffield Children's Hospital, Sheffield, UK.
  • Salman NJ; Tawam Hospital, Al Ain, United Arab Emirates.
  • Taylor J; Prevea Health Clinic, Hospital Sisters Health System St Vincent Hospital, Green Bay, WI, USA.
  • Phillips D; Division of Physical Therapy, University of North Carolina, Chapel Hill, NC, USA.
  • McGinn M; Royal Belfast Hospital for Sick Children, Belfast, UK.
  • McAlister WH; Mallinckrodt Institute of Radiology, Washington University School of Medicine, St Louis, MO, USA.
Lancet Diabetes Endocrinol ; 7(2): 93-105, 2019 02.
Article em En | MEDLINE | ID: mdl-30558909

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Proteínas Recombinantes de Fusão / Calcificação Fisiológica / Imunoglobulina G / Desenvolvimento Infantil / Fosfatase Alcalina / Hipofosfatasia Limite: Child / Child, preschool / Female / Humans / Infant / Male / Newborn Idioma: En Revista: Lancet Diabetes Endocrinol Ano de publicação: 2019 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Proteínas Recombinantes de Fusão / Calcificação Fisiológica / Imunoglobulina G / Desenvolvimento Infantil / Fosfatase Alcalina / Hipofosfatasia Limite: Child / Child, preschool / Female / Humans / Infant / Male / Newborn Idioma: En Revista: Lancet Diabetes Endocrinol Ano de publicação: 2019 Tipo de documento: Article