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Respiratory muscle training (RMT) in late-onset Pompe disease (LOPD): A protocol for a sham-controlled clinical trial.
Jones, Harrison N; Kuchibhatla, Maragatha; Crisp, Kelly D; Hobson Webb, Lisa D; Case, Laura; Batten, Milisa T; Marcus, Jill A; Kravitz, Richard M; Kishnani, Priya S.
Afiliação
  • Jones HN; Department of Surgery, Division of Head and Neck Surgery & Communication Sciences, Duke University Medical Center, Durham, NC, USA; Department of Speech Pathology and Audiology, Duke University Medical Center, Durham, NC, USA. Electronic address: harrison.jones@duke.edu.
  • Kuchibhatla M; Department of Biostatistics and Bioinformatics, Duke University Medical Center, Durham, NC, USA.
  • Crisp KD; Department of Surgery, Division of Head and Neck Surgery & Communication Sciences, Duke University Medical Center, Durham, NC, USA.
  • Hobson Webb LD; Department of Neurology, Neuromuscular Division, Duke University Medical Center, Durham, NC, USA.
  • Case L; Division of Physical Therapy, Duke University School Of Medicine, Durham, NC, USA.
  • Batten MT; Department of Speech Pathology and Audiology, Duke University Medical Center, Durham, NC, USA.
  • Marcus JA; Department of Speech Pathology and Audiology, Duke University Medical Center, Durham, NC, USA.
  • Kravitz RM; Division of Pediatric Pulmonary and Sleep Medicine, Duke University Medical Center, Durham, NC, USA.
  • Kishnani PS; Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, Durham, NC, USA.
Mol Genet Metab ; 127(4): 346-354, 2019 08.
Article em Es | MEDLINE | ID: mdl-31303277

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Exercícios Respiratórios / Doença de Depósito de Glicogênio Tipo II Tipo de estudo: Clinical_trials / Guideline Limite: Adult / Humans Idioma: Es Revista: Mol Genet Metab Assunto da revista: BIOLOGIA MOLECULAR / BIOQUIMICA / METABOLISMO Ano de publicação: 2019 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Exercícios Respiratórios / Doença de Depósito de Glicogênio Tipo II Tipo de estudo: Clinical_trials / Guideline Limite: Adult / Humans Idioma: Es Revista: Mol Genet Metab Assunto da revista: BIOLOGIA MOLECULAR / BIOQUIMICA / METABOLISMO Ano de publicação: 2019 Tipo de documento: Article