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GLPG2737 in lumacaftor/ivacaftor-treated CF subjects homozygous for the F508del mutation: A randomized phase 2A trial (PELICAN).
van Koningsbruggen-Rietschel, Silke; Conrath, Katja; Fischer, Rainald; Sutharsan, Sivagurunathan; Kempa, Axel; Gleiber, Wolfgang; Schwarz, Carsten; Hector, Andreas; Van Osselaer, Nancy; Pano, Arian; Corveleyn, Sam; Bwirire, Dieudonné; Santermans, Eva; Muller, Karine; Bellaire, Susan; Van de Steen, Olivier.
Afiliação
  • van Koningsbruggen-Rietschel S; Cystic Fibrosis Center, Children's Hospital, University of Cologne, Faculty of Medicine and University Hospital Cologne, Germany. Electronic address: Silke.vanKoningsbruggen@uk-koeln.de.
  • Conrath K; Galapagos NV, Mechelen, Belgium.
  • Fischer R; Cystic Fibrosis Center Munich-West, Munich, Germany.
  • Sutharsan S; Cystic Fibrosis Division, Department of Pulmonary Medicine, University of Essen, University Duisburg-Essen, Ruhrlandklinik, Germany.
  • Kempa A; Cystic Fibrosis Center, Klinikum Stuttgart, Stuttgart, Germany.
  • Gleiber W; Cystic Fibrosis Center, Department of Pulmonary Medicine, University Hospital, Goethe University, Frankfurt, Germany.
  • Schwarz C; Cystic Fibrosis Center, Charité - Universitätsmedizin, Berlin, Germany.
  • Hector A; Children's Hospital of the University of Tübingen, Tübingen, Germany.
  • Van Osselaer N; Galapagos NV, Mechelen, Belgium.
  • Pano A; Galapagos NV, Mechelen, Belgium.
  • Corveleyn S; Galapagos NV, Mechelen, Belgium.
  • Bwirire D; Galapagos NV, Mechelen, Belgium.
  • Santermans E; Galapagos NV, Mechelen, Belgium.
  • Muller K; Galapagos NV, Mechelen, Belgium.
  • Bellaire S; Galapagos BV, Leiden, The Netherlands.
  • Van de Steen O; Galapagos NV, Mechelen, Belgium.
J Cyst Fibros ; 19(2): 292-298, 2020 03.
Article em En | MEDLINE | ID: mdl-31594690

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Testes de Função Respiratória / Quinolonas / Regulador de Condutância Transmembrana em Fibrose Cística / Fibrose Cística / Benzodioxóis / Aminofenóis / Aminopiridinas Tipo de estudo: Clinical_trials / Prognostic_studies Limite: Adult / Female / Humans / Male Idioma: En Revista: J Cyst Fibros Ano de publicação: 2020 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Testes de Função Respiratória / Quinolonas / Regulador de Condutância Transmembrana em Fibrose Cística / Fibrose Cística / Benzodioxóis / Aminofenóis / Aminopiridinas Tipo de estudo: Clinical_trials / Prognostic_studies Limite: Adult / Female / Humans / Male Idioma: En Revista: J Cyst Fibros Ano de publicação: 2020 Tipo de documento: Article