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The road to biosimilars in rare diseases - ongoing lessons from Gaucher disease.
Drelichman, Guillermo; Castañeda-Hernández, Gilberto; Cem Ar, Muhlis; Dragosky, Marta; Garcia, Ricardo; Lee, Howard; Moiseev, Sergey; Naderi, Majid; Rosenbaum, Hanna; Znidar, Irena; Zuluaga, Andrés Felipe; Freisens, Selena; Mistry, Pramod K.
Afiliação
  • Drelichman G; Hospital de Niños Ricardo Gutiérrez, Buenos Aires, Argentina.
  • Castañeda-Hernández G; Departamento de Farmacología, Centro de Investigación y de Estudios Avanzados del Instituto Politécnico Nacional, Mexico City, Mexico.
  • Cem Ar M; Division of Hematology, Department of Internal Medicine, Istanbul University-Cerrahpasa, Cerrahpasa Faculty of Medicine, Istanbul, Turkey.
  • Dragosky M; Departamento de Oncohematología, Henry Moore Institute, Buenos Aires, Argentina.
  • Garcia R; Centro Latino Americano de Pesquisa em Biológicos, São Paulo, Brazil.
  • Lee H; Department of Clinical Pharmacology and Therapeutics, Seoul National University College of Medicine and Hospital, Graduate School of Convergence Science and Technology, Seoul National University, South Korea.
  • Moiseev S; Tareev Clinic of Internal Diseases, Sechenov First Moscow State Medical University, Moscow, Russia.
  • Naderi M; Genetic Research Center in Non-Communicable Disease, Zahedan University of Medical Sciences, Zahedan, Iran.
  • Rosenbaum H; Hematology Clinic, Clalit services, Nazareth Towers, Israel.
  • Znidar I; International Gaucher Alliance, Dursley, UK.
  • Zuluaga AF; Departamento de Farmacologia y Toxicologia, Facultad de Medicina, Universidad de Antioquia, Medellín, Colombia.
  • Freisens S; Global Medical Affairs, Sanofi Genzyme, Cambridge, Massachusetts.
  • Mistry PK; Department of Medicine, Yale University School of Medicine, New Haven, Connecticut.
Am J Hematol ; 95(3): 233-237, 2020 03.
Article em En | MEDLINE | ID: mdl-31816110

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Medicamentos Biossimilares / Doença de Gaucher Limite: Humans Idioma: En Revista: Am J Hematol Ano de publicação: 2020 Tipo de documento: Article País de afiliação: Argentina

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Medicamentos Biossimilares / Doença de Gaucher Limite: Humans Idioma: En Revista: Am J Hematol Ano de publicação: 2020 Tipo de documento: Article País de afiliação: Argentina