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Dual Supramolecular Nanoparticle Vectors Enable CRISPR/Cas9-Mediated Knockin of Retinoschisin 1 Gene-A Potential Nonviral Therapeutic Solution for X-Linked Juvenile Retinoschisis.
Chou, Shih-Jie; Yang, Peng; Ban, Qian; Yang, Yi-Ping; Wang, Mong-Lien; Chien, Chian-Shiu; Chen, Shih-Jen; Sun, Na; Zhu, Yazhen; Liu, Hongtao; Hui, Wenqiao; Lin, Tai-Chi; Wang, Fang; Zhang, Ryan Yue; Nguyen, Viet Q; Liu, Wenfei; Chen, Mengxiang; Jonas, Steve J; Weiss, Paul S; Tseng, Hsian-Rong; Chiou, Shih-Hwa.
Afiliação
  • Chou SJ; Division of Basic Research Department of Medical Research and Department of Ophthalmology Taipei Veterans General Hospital Taipei 112 Taiwan.
  • Yang P; Institute of Pharmacology School of Medicine National Yang-Ming University Taipei 112 Taiwan.
  • Ban Q; Department of Molecular and Medical Pharmacology Crump Institute for Molecular Imaging (CIMI) California NanoSystems Institute (CNSI) University of California, Los Angeles Los Angeles CA 90095 USA.
  • Yang YP; Center for Stem Cell and Translational Medicine School of Life Sciences Anhui University Hefei 230601 China.
  • Wang ML; Department of Medical Research Taipei Veterans General Hospital Taipei 112 Taiwan.
  • Chien CS; School of Medicine, and School of Pharmaceutical Sciences National Yang-Ming University Taipei 112 Taiwan.
  • Chen SJ; Institute of Pharmacology School of Medicine National Yang-Ming University Taipei 112 Taiwan.
  • Sun N; Department of Medical Research Taipei Veterans General Hospital Taipei 112 Taiwan.
  • Zhu Y; Institute of Food Safety and Health Risk Assessment National Yang Ming University Taipei 112 Taiwan.
  • Liu H; Division of Basic Research Department of Medical Research and Department of Ophthalmology Taipei Veterans General Hospital Taipei 112 Taiwan.
  • Hui W; Institute of Pharmacology School of Medicine National Yang-Ming University Taipei 112 Taiwan.
  • Lin TC; Division of Basic Research Department of Medical Research and Department of Ophthalmology Taipei Veterans General Hospital Taipei 112 Taiwan.
  • Wang F; Institute of Pharmacology School of Medicine National Yang-Ming University Taipei 112 Taiwan.
  • Zhang RY; Department of Molecular and Medical Pharmacology Crump Institute for Molecular Imaging (CIMI) California NanoSystems Institute (CNSI) University of California, Los Angeles Los Angeles CA 90095 USA.
  • Nguyen VQ; Department of Molecular and Medical Pharmacology Crump Institute for Molecular Imaging (CIMI) California NanoSystems Institute (CNSI) University of California, Los Angeles Los Angeles CA 90095 USA.
  • Liu W; Shandong Provincial Qianfoshan Hospital the First Hospital Affiliated to Shandong First Medical University Jinan 250014 China.
  • Chen M; Institute of Animal Husbandry and Veterinary Medicine Anhui Academy of Agriculture Sciences Hefei 230031 China.
  • Jonas SJ; Division of Basic Research Department of Medical Research and Department of Ophthalmology Taipei Veterans General Hospital Taipei 112 Taiwan.
  • Weiss PS; Institute of Pharmacology School of Medicine National Yang-Ming University Taipei 112 Taiwan.
  • Tseng HR; State Key Laboratory of Molecular Engineering of Polymers Department of Macromolecular Science Fudan University Shanghai 200433 China.
  • Chiou SH; Department of Molecular and Medical Pharmacology Crump Institute for Molecular Imaging (CIMI) California NanoSystems Institute (CNSI) University of California, Los Angeles Los Angeles CA 90095 USA.
Adv Sci (Weinh) ; 7(10): 1903432, 2020 May.
Article em En | MEDLINE | ID: mdl-32440478

Texto completo: 1 Base de dados: MEDLINE Idioma: En Revista: Adv Sci (Weinh) Ano de publicação: 2020 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Idioma: En Revista: Adv Sci (Weinh) Ano de publicação: 2020 Tipo de documento: Article