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Development of AAV Variants with Human Hepatocyte Tropism and Neutralizing Antibody Escape Capacity.
Pei, Xiaolei; Shao, Wenwei; Xing, Allene; Askew, Charles; Chen, Xiaojing; Cui, Caibin; Abajas, Yasmina L; Gerber, David A; Merricks, Elizabeth P; Nichols, Timothy C; Li, Wuping; Samulski, R Jude; Li, Chengwen.
Afiliação
  • Pei X; Institute of Hematology and Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin 300020, China.
  • Shao W; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.
  • Xing A; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.
  • Askew C; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.
  • Chen X; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.
  • Cui C; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.
  • Abajas YL; Department of Surgery, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.
  • Gerber DA; Department of Pediatrics, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.
  • Merricks EP; Department of Surgery, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.
  • Nichols TC; Department of Pathology and Laboratory Medicine, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.
  • Li W; Department of Pathology and Laboratory Medicine, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.
  • Samulski RJ; Institute of Pathogen Biology, Chinese Academy of Medical Sciences & Peking Union Medical College, Beijing 100730, China.
  • Li C; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.
Mol Ther Methods Clin Dev ; 18: 259-268, 2020 Sep 11.
Article em En | MEDLINE | ID: mdl-32637455

Texto completo: 1 Base de dados: MEDLINE Tipo de estudo: Prognostic_studies Idioma: En Revista: Mol Ther Methods Clin Dev Ano de publicação: 2020 Tipo de documento: Article País de afiliação: China

Texto completo: 1 Base de dados: MEDLINE Tipo de estudo: Prognostic_studies Idioma: En Revista: Mol Ther Methods Clin Dev Ano de publicação: 2020 Tipo de documento: Article País de afiliação: China