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First open-label, single-arm, prospective study of real-world use of FIX replacement therapy in a predominantly pediatric hemophilia B population in China.
Yang, Renchi; Wu, Runhui; Sun, Jing; Sun, Feifei; Rupon, Jeremy; Huard, Francois; Korth-Bradley, Joan M; Xu, Lihong; Luo, Binyu; Liu, Yingxue Cathy; Rendo, Pablo.
Afiliação
  • Yang R; Institute of Haematology and Blood Diseases Hospital, Chinese Academy of Medical Sciences, Tianjin.
  • Wu R; Hematology Oncology Centre, Beijing Children's Hospital, Capital Medical University, Beijing.
  • Sun J; Nanfang Hospital, Southern Medical University, Guangzhou.
  • Sun F; Pfizer (China) Research & Development Co, Ltd, Shanghai, China.
  • Rupon J; Pfizer Inc, Collegeville, PA.
  • Huard F; Pfizer PIO, Paris, France.
  • Korth-Bradley JM; Pfizer Inc, Collegeville, PA.
  • Xu L; Pfizer (China) Research & Development Co, Ltd, Shanghai, China.
  • Luo B; Pfizer (China) Research & Development Co, Ltd, Shanghai, China.
  • Liu YC; Pfizer (China) Research & Development Co, Ltd, Shanghai, China.
  • Rendo P; Pfizer Inc, Collegeville, PA.
Medicine (Baltimore) ; 100(21): e26077, 2021 May 28.
Article em En | MEDLINE | ID: mdl-34032739

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Fator IX / Hemofilia B / Terapia de Reposição de Enzimas / Hemorragia Tipo de estudo: Clinical_trials / Etiology_studies / Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Adolescent / Child / Child, preschool / Humans / Infant / Male País/Região como assunto: Asia Idioma: En Revista: Medicine (Baltimore) Ano de publicação: 2021 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Fator IX / Hemofilia B / Terapia de Reposição de Enzimas / Hemorragia Tipo de estudo: Clinical_trials / Etiology_studies / Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Adolescent / Child / Child, preschool / Humans / Infant / Male País/Região como assunto: Asia Idioma: En Revista: Medicine (Baltimore) Ano de publicação: 2021 Tipo de documento: Article