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Translational and clinical pharmacology considerations in drug repurposing for X-linked adrenoleukodystrophy-A rare peroxisomal disorder.
Tieu, Julianne H; Sahasrabudhe, Siddhee A; Orchard, Paul J; Cloyd, James C; Kartha, Reena V.
Afiliação
  • Tieu JH; Center for Orphan Drug Research, Department of Experimental and Clinical Pharmacology, College of Pharmacy, University of Minnesota, Minneapolis, Minnesota, USA.
  • Sahasrabudhe SA; Center for Orphan Drug Research, Department of Experimental and Clinical Pharmacology, College of Pharmacy, University of Minnesota, Minneapolis, Minnesota, USA.
  • Orchard PJ; Division of Pediatric Blood and Marrow Transplantation, Department of Pediatrics, Medical School, University of Minnesota, Minneapolis, Minnesota, USA.
  • Cloyd JC; Center for Orphan Drug Research, Department of Experimental and Clinical Pharmacology, College of Pharmacy, University of Minnesota, Minneapolis, Minnesota, USA.
  • Kartha RV; Center for Orphan Drug Research, Department of Experimental and Clinical Pharmacology, College of Pharmacy, University of Minnesota, Minneapolis, Minnesota, USA.
Br J Clin Pharmacol ; 88(6): 2552-2563, 2022 06.
Article em En | MEDLINE | ID: mdl-34558098

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Farmacologia Clínica / Adrenoleucodistrofia Limite: Humans Idioma: En Revista: Br J Clin Pharmacol Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Estados Unidos

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Farmacologia Clínica / Adrenoleucodistrofia Limite: Humans Idioma: En Revista: Br J Clin Pharmacol Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Estados Unidos