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Human iPSC-derived astrocytes generated from donors with globoid cell leukodystrophy display phenotypes associated with disease.
Lieberman, Richard; Cortes, Leslie K; Gao, Grace; Park, Hyejung; Wang, Bing; Jones, Patrick L; Hunter, R Bridge; Leonard, John P; Barker, Robert H.
Afiliação
  • Lieberman R; Lysosomal Storage and Metabolic Disease Cluster, Rare and Neurologic Disease Therapeutic Area, Sanofi, Framingham, MA, United States of America.
  • Cortes LK; Lysosomal Storage and Metabolic Disease Cluster, Rare and Neurologic Disease Therapeutic Area, Sanofi, Framingham, MA, United States of America.
  • Gao G; Lysosomal Storage and Metabolic Disease Cluster, Rare and Neurologic Disease Therapeutic Area, Sanofi, Framingham, MA, United States of America.
  • Park H; US Early Development, Sanofi, Waltham, MA, United States of America.
  • Wang B; US Early Development, Sanofi, Waltham, MA, United States of America.
  • Jones PL; Lysosomal Storage and Metabolic Disease Cluster, Rare and Neurologic Disease Therapeutic Area, Sanofi, Framingham, MA, United States of America.
  • Hunter RB; Lysosomal Storage and Metabolic Disease Cluster, Rare and Neurologic Disease Therapeutic Area, Sanofi, Framingham, MA, United States of America.
  • Leonard JP; Lysosomal Storage and Metabolic Disease Cluster, Rare and Neurologic Disease Therapeutic Area, Sanofi, Framingham, MA, United States of America.
  • Barker RH; Lysosomal Storage and Metabolic Disease Cluster, Rare and Neurologic Disease Therapeutic Area, Sanofi, Framingham, MA, United States of America.
PLoS One ; 17(8): e0271360, 2022.
Article em En | MEDLINE | ID: mdl-35921286

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Células-Tronco Pluripotentes Induzidas / Leucodistrofia de Células Globoides Tipo de estudo: Prognostic_studies / Risk_factors_studies Limite: Animals / Humans Idioma: En Revista: PLoS One Assunto da revista: CIENCIA / MEDICINA Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Estados Unidos

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Células-Tronco Pluripotentes Induzidas / Leucodistrofia de Células Globoides Tipo de estudo: Prognostic_studies / Risk_factors_studies Limite: Animals / Humans Idioma: En Revista: PLoS One Assunto da revista: CIENCIA / MEDICINA Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Estados Unidos