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Thiomorpholino oligonucleotides as a robust class of next generation platforms for alternate mRNA splicing.
Le, Bao T; Paul, Sibasish; Jastrzebska, Katarzyna; Langer, Heera; Caruthers, Marvin H; Veedu, Rakesh N.
Afiliação
  • Le BT; Centre for Molecular Medicine and Innovative Therapeutics, Murdoch University, Murdoch, Perth, WA 6150, Australia.
  • Paul S; Perron Institute for Neurological and Translational Science, Nedlands, Perth, WA 6009, Australia.
  • Jastrzebska K; Nucleic Acid Solutions Division, Agilent Technologies, Boulder, CO 80301.
  • Langer H; Centre of Molecular and Macromolecular Studies, Polish Academy of Sciences, 90-363 Lodz, Poland.
  • Caruthers MH; Department of Biochemistry, University of Colorado, Boulder, CO 80309.
  • Veedu RN; Department of Biochemistry, University of Colorado, Boulder, CO 80309.
Proc Natl Acad Sci U S A ; 119(36): e2207956119, 2022 09 06.
Article em En | MEDLINE | ID: mdl-36037350

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Terapia Genética / Splicing de RNA / Distrofia Muscular de Duchenne / Morfolinos Limite: Animals Idioma: En Revista: Proc Natl Acad Sci U S A Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Austrália

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Terapia Genética / Splicing de RNA / Distrofia Muscular de Duchenne / Morfolinos Limite: Animals Idioma: En Revista: Proc Natl Acad Sci U S A Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Austrália