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Efficacy and safety of the B-domain-deleted TQG202 for on-demand treatment in moderate and severe haemophilia A patients: A multicentre, single-arm trial.
Sun, Zimin; Xi, Yaming; Liu, Wei; Yang, Linhua; Wang, Xuefeng; Jin, Chenghao; Jia, Haifei; Zhang, Lei.
Afiliação
  • Sun Z; Department of Hematology, The Affiliated Provincial Hospital of Anhui Medical University, Hefei, Anhui, China.
  • Xi Y; Department of Hematology, The First Hospital of Lanzhou University, Lanzhou, Gansu, China.
  • Liu W; State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Tianjin Key Laboratory of Gene Therapy for Blood Diseases, CAMS Key Laboratory of Gene Therapy for Blood Diseases, Institute of Hematology & Blood Diseases H
  • Yang L; Department of Hematology, The Second Hospital of Shanxi Medical University, Taiyuan, Shanxi, China.
  • Wang X; Ruijin Hospital, Shanghai Jiaotong University Medical School, Shanghai, China.
  • Jin C; Hemophilia Information Management Center of Jiangxi Province, Jiangxi Provincial People's Hospital, Nanchang, Jiangxi, China.
  • Jia H; R&D Institute, Chia Tai Tianqing Pharmaceutical Group Co. Ltd., Nanjing, Jiangsu, China.
  • Zhang L; State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Tianjin Key Laboratory of Gene Therapy for Blood Diseases, CAMS Key Laboratory of Gene Therapy for Blood Diseases, Institute of Hematology & Blood Diseases H
Haemophilia ; 29(4): 997-1004, 2023 Jul.
Article em En | MEDLINE | ID: mdl-36913439

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Hemostáticos / Hemofilia A Tipo de estudo: Clinical_trials / Incidence_studies / Prognostic_studies Limite: Adolescent / Adult / Child / Humans / Middle aged País/Região como assunto: Asia Idioma: En Revista: Haemophilia Assunto da revista: HEMATOLOGIA Ano de publicação: 2023 Tipo de documento: Article País de afiliação: China

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Hemostáticos / Hemofilia A Tipo de estudo: Clinical_trials / Incidence_studies / Prognostic_studies Limite: Adolescent / Adult / Child / Humans / Middle aged País/Região como assunto: Asia Idioma: En Revista: Haemophilia Assunto da revista: HEMATOLOGIA Ano de publicação: 2023 Tipo de documento: Article País de afiliação: China