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Real-world safety and effectiveness of elexacaftor/tezacaftor/ivacaftor in people with cystic fibrosis: Interim results of a long-term registry-based study.
Bower, Julie K; Volkova, Nataliya; Ahluwalia, Neil; Sahota, Gurvaneet; Xuan, Fengjuan; Chin, Anna; Weinstock, Tanya G; Ostrenga, Josh; Elbert, Alexander.
Afiliação
  • Bower JK; Vertex Pharmaceuticals Incorporated, Boston, MA, United States of America. Electronic address: Julie_Bower@vrtx.com.
  • Volkova N; Vertex Pharmaceuticals Incorporated, Boston, MA, United States of America.
  • Ahluwalia N; Vertex Pharmaceuticals Incorporated, Boston, MA, United States of America.
  • Sahota G; Vertex Pharmaceuticals Incorporated, Boston, MA, United States of America.
  • Xuan F; Vertex Pharmaceuticals Incorporated, Boston, MA, United States of America.
  • Chin A; Vertex Pharmaceuticals Incorporated, Boston, MA, United States of America.
  • Weinstock TG; Vertex Pharmaceuticals Incorporated, Boston, MA, United States of America.
  • Ostrenga J; Cystic Fibrosis Foundation, Bethesda, MD, United States of America.
  • Elbert A; Cystic Fibrosis Foundation, Bethesda, MD, United States of America.
J Cyst Fibros ; 22(4): 730-737, 2023 07.
Article em En | MEDLINE | ID: mdl-36963986

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Fibrose Cística Tipo de estudo: Diagnostic_studies / Prognostic_studies / Risk_factors_studies Limite: Humans Idioma: En Revista: J Cyst Fibros Ano de publicação: 2023 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Fibrose Cística Tipo de estudo: Diagnostic_studies / Prognostic_studies / Risk_factors_studies Limite: Humans Idioma: En Revista: J Cyst Fibros Ano de publicação: 2023 Tipo de documento: Article