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AAV Gene Augmentation of Truncated Complement Factor H Differentially Rescues Ocular Complement Dysregulation in a Mouse Model.
Grigsby, Daniel; Klingeborn, Mikael; Kelly, Una; Chew, Lindsey A; Asokan, Aravind; Devlin, Garth; Smith, Sharon; Keyes, Lisa; Timmers, Adrian; Scaria, Abraham; Bowes Rickman, Catherine.
Afiliação
  • Grigsby D; Department of Ophthalmology, Duke University School of Medicine, Durham, North Carolina, United States.
  • Klingeborn M; Department of Ophthalmology, Duke University School of Medicine, Durham, North Carolina, United States.
  • Kelly U; McLaughlin Research Institute, Great Falls, Montana, United States.
  • Chew LA; Department of Ophthalmology, Duke University School of Medicine, Durham, North Carolina, United States.
  • Asokan A; Department of Ophthalmology, Duke University School of Medicine, Durham, North Carolina, United States.
  • Devlin G; Department of Cell Biology, Duke University School of Medicine, Durham, North Carolina, United States.
  • Smith S; Departments of Surgery, Molecular Genetics and Microbiology, and Biomedical Engineering, Duke University School of Medicine, Durham, North Carolina, United States.
  • Keyes L; Departments of Surgery, Molecular Genetics and Microbiology, and Biomedical Engineering, Duke University School of Medicine, Durham, North Carolina, United States.
  • Timmers A; Applied Genetic Technologies Corporation, Alachua, Florida, United States.
  • Scaria A; Pfizer, Morrisville, North Carolina, United States.
  • Bowes Rickman C; Editas Medicine, Cambridge, Massachusetts, United States.
Invest Ophthalmol Vis Sci ; 64(10): 25, 2023 07 03.
Article em En | MEDLINE | ID: mdl-37471073

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Fator H do Complemento / Degeneração Macular Tipo de estudo: Prognostic_studies Limite: Animals / Humans Idioma: En Revista: Invest Ophthalmol Vis Sci Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Estados Unidos

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Fator H do Complemento / Degeneração Macular Tipo de estudo: Prognostic_studies Limite: Animals / Humans Idioma: En Revista: Invest Ophthalmol Vis Sci Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Estados Unidos