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Sortilin inhibition treats multiple neurodegenerative lysosomal storage disorders.
Leppert, Hannah G; Anderson, Joelle T; Timm, Kaylie J; Davoli, Cristina; Pratt, Melissa A; Booth, Clarissa D; White, Katherine A; Rechtzigel, Mitchell J; Meyerink, Brandon L; Johnson, Tyler B; Brudvig, Jon J; Weimer, Jill M.
Afiliação
  • Leppert HG; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD.
  • Anderson JT; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD.
  • Timm KJ; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD.
  • Davoli C; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD.
  • Pratt MA; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD.
  • Booth CD; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD.
  • White KA; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD.
  • Rechtzigel MJ; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD.
  • Meyerink BL; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD.
  • Johnson TB; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD.
  • Brudvig JJ; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD.
  • Weimer JM; Department of Pediatrics, Sanford School of Medicine, University of South Dakota, Sioux Falls, SD, USA.
bioRxiv ; 2023 Sep 22.
Article em En | MEDLINE | ID: mdl-37790379

Texto completo: 1 Base de dados: MEDLINE Tipo de estudo: Prognostic_studies Idioma: En Revista: BioRxiv Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Sudão

Texto completo: 1 Base de dados: MEDLINE Tipo de estudo: Prognostic_studies Idioma: En Revista: BioRxiv Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Sudão