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Cystic fibrosis transmembrane conductance regulator modulator administration to a F508del heterozygous infant with meconium pseudocyst and short bowel syndrome: A case report.
Stoffella, Sylvia; Ly, Ngoc; McGarry, Meghan; Neemuchwala, Fatima; Church, Gwynne; Chan, Marilynn; Cuneo, Addison; Omori, Makiko; Gibb, Elizabeth.
Afiliação
  • Stoffella S; Department of Pharmacy, University of California San Francisco, San Francisco, California, USA.
  • Ly N; Department of Pediatrics, University of California San Francisco, San Francisco, California, USA.
  • McGarry M; Department of Pediatrics, University of California San Francisco, San Francisco, California, USA.
  • Neemuchwala F; Department of Pediatrics, University of California San Francisco, San Francisco, California, USA.
  • Church G; Department of Pediatrics, University of California San Francisco, San Francisco, California, USA.
  • Chan M; Department of Pediatrics, University of California San Francisco, San Francisco, California, USA.
  • Cuneo A; Department of Pediatrics, University of California San Francisco, San Francisco, California, USA.
  • Omori M; Department of Pediatrics, University of California San Francisco, San Francisco, California, USA.
  • Gibb E; Department of Pediatrics, University of California San Francisco, San Francisco, California, USA.
Pediatr Pulmonol ; 59(3): 791-793, 2024 Mar.
Article em En | MEDLINE | ID: mdl-38088240

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Síndrome do Intestino Curto / Fibrose Cística Limite: Humans / Newborn Idioma: En Revista: Pediatr Pulmonol Assunto da revista: PEDIATRIA Ano de publicação: 2024 Tipo de documento: Article País de afiliação: Estados Unidos

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Síndrome do Intestino Curto / Fibrose Cística Limite: Humans / Newborn Idioma: En Revista: Pediatr Pulmonol Assunto da revista: PEDIATRIA Ano de publicação: 2024 Tipo de documento: Article País de afiliação: Estados Unidos