Expanded-access use of elamipretide in a patient with membrane protein-associated neurodegeneration.
Clin Case Rep
; 12(7): e9116, 2024 Jul.
Article
em En
| MEDLINE
| ID: mdl-38919884
ABSTRACT
This case report presents a progressively declining 17-year-old patient with membrane protein-associated neurodegeneration who demonstrated symptomatic improvements in her dysarthria, dysphagia, and gait, and objective improvements in her 6-minute walk test and 5 times sit-to-stand test during elamipretide treatment.
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Base de dados:
MEDLINE
Idioma:
En
Revista:
Clin Case Rep
Ano de publicação:
2024
Tipo de documento:
Article