Detalhe da pesquisa
1.
Genomic investigations of unexplained acute hepatitis in children.
Nature
; 617(7961): 564-573, 2023 May.
Artigo
em Inglês
| MEDLINE | ID: mdl-36996872
2.
Production of lentiviral vectors using novel, enzymatically produced, linear DNA.
Gene Ther
; 26(3-4): 86-92, 2019 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-30643205
3.
One transgene, two myopathies: an MTM1 'cross gene therapy' for BIN1 deficiency?
Brain
; 146(10): 3966-3968, 2023 10 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-37738144
4.
Eliminating HIV-1 Packaging Sequences from Lentiviral Vector Proviruses Enhances Safety and Expedites Gene Transfer for Gene Therapy.
Mol Ther
; 25(8): 1790-1804, 2017 08 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-28550974
5.
Urokinase-type plasminogen activator (uPA) regulates invasion and matrix remodelling in colorectal cancer.
Matrix Biol Plus
; 19-20: 100137, 2023 Dec.
Artigo
em Inglês
| MEDLINE | ID: mdl-38020586
6.
3D human induced pluripotent stem cell-derived bioengineered skeletal muscles for tissue, disease and therapy modeling.
Nat Protoc
; 18(4): 1337-1376, 2023 04.
Artigo
em Inglês
| MEDLINE | ID: mdl-36792780
7.
Re-structuring lentiviral vectors to express genomic RNA via cap-dependent translation.
Mol Ther Methods Clin Dev
; 20: 357-365, 2021 Mar 12.
Artigo
em Inglês
| MEDLINE | ID: mdl-33553484
8.
In Vitro and In Vivo Evaluation of Human Adenovirus Type 49 as a Vector for Therapeutic Applications.
Viruses
; 13(8)2021 07 28.
Artigo
em Inglês
| MEDLINE | ID: mdl-34452348
9.
Dystrophin involvement in peripheral circadian SRF signalling.
Life Sci Alliance
; 4(10)2021 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-34389686
10.
Gene therapy restores dopamine transporter expression and ameliorates pathology in iPSC and mouse models of infantile parkinsonism.
Sci Transl Med
; 13(594)2021 05 19.
Artigo
em Inglês
| MEDLINE | ID: mdl-34011628
11.
Effects of corticosterone within the hypothalamic arcuate nucleus on food intake and body weight in male rats.
Mol Metab
; 36: 100972, 2020 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-32229097
12.
An In Vitro Whole-Organ Liver Engineering for Testing of Genetic Therapies.
iScience
; 23(12): 101808, 2020 Dec 18.
Artigo
em Inglês
| MEDLINE | ID: mdl-33305175
13.
Generation of light-producing somatic-transgenic mice using adeno-associated virus vectors.
Sci Rep
; 10(1): 2121, 2020 02 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-32034258
14.
Non-canonical capsid engineering highlights new possibilities for AAV vectorology.
Mol Ther Methods Clin Dev
; 32(1): 101221, 2024 Mar 14.
Artigo
em Inglês
| MEDLINE | ID: mdl-38487107
15.
Foamy Virus Vectors Transduce Visceral Organs and Hippocampal Structures following In Vivo Delivery to Neonatal Mice.
Mol Ther Nucleic Acids
; 12: 626-634, 2018 Sep 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-30081233
16.
Erratum: Lentiviral vectors can be used for full-length dystrophin gene therapy.
Sci Rep
; 7: 46880, 2017 08 29.
Artigo
em Inglês
| MEDLINE | ID: mdl-28849794
17.
Lentiviral vectors can be used for full-length dystrophin gene therapy.
Sci Rep
; 7(1): 79, 2017 03 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-28250438
18.
Lentiviral vectors can be used for full-length dystrophin gene therapy.
Sci Rep
; 7: 44775, 2017 03 17.
Artigo
em Inglês
| MEDLINE | ID: mdl-28303972
19.
Continual conscious bioluminescent imaging in freely moving somatotransgenic mice.
Sci Rep
; 7(1): 6374, 2017 07 25.
Artigo
em Inglês
| MEDLINE | ID: mdl-28743959
20.
Autologous skeletal muscle derived cells expressing a novel functional dystrophin provide a potential therapy for Duchenne Muscular Dystrophy.
Sci Rep
; 6: 19750, 2016 Jan 27.
Artigo
em Inglês
| MEDLINE | ID: mdl-26813695