Detalhe da pesquisa
1.
Circulating hematopoietic stem/progenitor cell subsets contribute to human hematopoietic homeostasis.
Blood
; 143(19): 1937-1952, 2024 May 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-38446574
2.
Hematopoietic Stem- and Progenitor-Cell Gene Therapy for Hurler Syndrome.
N Engl J Med
; 385(21): 1929-1940, 2021 11 18.
Artigo
em Inglês
| MEDLINE | ID: mdl-34788506
3.
Follicular helper T cell signature of replicative exhaustion, apoptosis, and senescence in common variable immunodeficiency.
Eur J Immunol
; 52(7): 1171-1189, 2022 07.
Artigo
em Inglês
| MEDLINE | ID: mdl-35562849
4.
A Novel Assay in Whole Blood Demonstrates Restoration of Mitochondrial Activity in Phagocytes After Successful HSCT in Hyperinflamed X-Linked Chronic Granulomatous Disease.
J Clin Immunol
; 42(8): 1742-1747, 2022 11.
Artigo
em Inglês
| MEDLINE | ID: mdl-35945378
5.
Successful Treatment With Ledipasvir/Sofosbuvir in an Infant With Severe Combined Immunodeficiency Caused by Adenosine Deaminase Deficiency With HCV Allowed Gene Therapy with Strimvelis.
Hepatology
; 68(6): 2434-2437, 2018 12.
Artigo
em Inglês
| MEDLINE | ID: mdl-30014500
6.
Early skeletal outcomes after hematopoietic stem and progenitor cell gene therapy for Hurler syndrome.
Sci Transl Med
; 16(745): eadi8214, 2024 May.
Artigo
em Inglês
| MEDLINE | ID: mdl-38691622
7.
Long-term and real-world safety and efficacy of retroviral gene therapy for adenosine deaminase deficiency.
Nat Med
; 30(2): 488-497, 2024 Feb.
Artigo
em Inglês
| MEDLINE | ID: mdl-38355973
8.
Hematopoietic reconstitution dynamics of mobilized- and bone marrow-derived human hematopoietic stem cells after gene therapy.
Nat Commun
; 14(1): 3068, 2023 05 27.
Artigo
em Inglês
| MEDLINE | ID: mdl-37244942
9.
Wiskott-Aldrich syndrome: Oral findings and microbiota in children and review of the literature.
Clin Exp Dent Res
; 8(1): 28-36, 2022 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-35199474
10.
Bone marrow harvesting from paediatric patients undergoing haematopoietic stem cell gene therapy.
Bone Marrow Transplant
; 54(12): 1995-2003, 2019 12.
Artigo
em Inglês
| MEDLINE | ID: mdl-31150018