Detalhe da pesquisa
1.
Gene Therapy in Patients with the Crigler-Najjar Syndrome.
N Engl J Med
; 389(7): 620-631, 2023 Aug 17.
Artigo
em Inglês
| MEDLINE | ID: mdl-37585628
2.
Analysis of Adeno-Associated Virus Serotype 8 (AAV8)-antibody complexes using epitope mapping by molecular imprinting leads to the identification of Fab peptides that potentially evade AAV8 neutralisation.
Nanomedicine
; 52: 102691, 2023 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-37329939
3.
Smartphone LiDAR Data: A Case Study for Numerisation of Indoor Buildings in Railway Stations.
Sensors (Basel)
; 23(4)2023 Feb 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-36850565
4.
H-BIM and Artificial Intelligence: Classification of Architectural Heritage for Semi-Automatic Scan-to-BIM Reconstruction.
Sensors (Basel)
; 23(5)2023 Feb 23.
Artigo
em Inglês
| MEDLINE | ID: mdl-36904701
5.
Early Phase Clinical Immunogenicity of Valoctocogene Roxaparvovec, an AAV5-Mediated Gene Therapy for Hemophilia A.
Mol Ther
; 29(2): 597-610, 2021 02 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-33309883
6.
Prevalence and long-term monitoring of humoral immunity against adeno-associated virus in Duchenne Muscular Dystrophy patients.
Cell Immunol
; 342: 103780, 2019 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-29571923
7.
Systemic AAV8-Mediated Gene Therapy Drives Whole-Body Correction of Myotubular Myopathy in Dogs.
Mol Ther
; 25(4): 839-854, 2017 04 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-28237839
8.
Forelimb treatment in a large cohort of dystrophic dogs supports delivery of a recombinant AAV for exon skipping in Duchenne patients.
Mol Ther
; 22(11): 1923-35, 2014 Nov.
Artigo
em Inglês
| MEDLINE | ID: mdl-25200009
9.
Humoral and cellular capsid-specific immune responses to adeno-associated virus type 1 in randomized healthy donors.
J Immunol
; 188(12): 6418-24, 2012 Jun 15.
Artigo
em Inglês
| MEDLINE | ID: mdl-22593612
10.
Efficacy, pharmacokinetics, and safety in the mouse and primate retina of dual AAV vectors for Usher syndrome type 1B.
Mol Ther Methods Clin Dev
; 28: 396-411, 2023 Mar 09.
Artigo
em Inglês
| MEDLINE | ID: mdl-36910588
11.
A 10 patient case report on the impact of plasmapheresis upon neutralizing factors against adeno-associated virus (AAV) types 1, 2, 6, and 8.
Mol Ther
; 19(11): 2084-91, 2011 Nov.
Artigo
em Inglês
| MEDLINE | ID: mdl-21629225
12.
Liver-Directed Adeno-Associated Virus-Mediated Gene Therapy for Mucopolysaccharidosis Type VI.
NEJM Evid
; 1(7): EVIDoa2200052, 2022 Jul.
Artigo
em Inglês
| MEDLINE | ID: mdl-38319253
13.
Capsid-specific removal of circulating antibodies to adeno-associated virus vectors.
Sci Rep
; 10(1): 864, 2020 01 21.
Artigo
em Inglês
| MEDLINE | ID: mdl-31965041
14.
Highly efficient transduction of human plasmacytoid dendritic cells without phenotypic and functional maturation.
J Transl Med
; 7: 10, 2009 Jan 27.
Artigo
em Inglês
| MEDLINE | ID: mdl-19173717
15.
Prevalence and Relevance of Pre-Existing Anti-Adeno-Associated Virus Immunity in the Context of Gene Therapy for Crigler-Najjar Syndrome.
Hum Gene Ther
; 30(10): 1297-1305, 2019 10.
Artigo
em Inglês
| MEDLINE | ID: mdl-31502485
16.
Preclinical Development of an AAV8-hUGT1A1 Vector for the Treatment of Crigler-Najjar Syndrome.
Mol Ther Methods Clin Dev
; 12: 157-174, 2019 Mar 15.
Artigo
em Inglês
| MEDLINE | ID: mdl-30705921
17.
Exposure to wild-type AAV drives distinct capsid immunity profiles in humans.
J Clin Invest
; 128(12): 5267-5279, 2018 12 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-30352429
18.
Long-term microdystrophin gene therapy is effective in a canine model of Duchenne muscular dystrophy.
Nat Commun
; 8: 16105, 2017 07 25.
Artigo
em Inglês
| MEDLINE | ID: mdl-28742067
19.
A translationally optimized AAV-UGT1A1 vector drives safe and long-lasting correction of Crigler-Najjar syndrome.
Mol Ther Methods Clin Dev
; 3: 16049, 2016.
Artigo
em Inglês
| MEDLINE | ID: mdl-27722180
20.
Determination of anti-adeno-associated virus vector neutralizing antibody titer with an in vitro reporter system.
Hum Gene Ther Methods
; 26(2): 45-53, 2015 Apr.
Artigo
em Inglês
| MEDLINE | ID: mdl-25819687