Your browser doesn't support javascript.
loading
DUX4 Transcript Knockdown with Antisense 2'-O-Methoxyethyl Gapmers for the Treatment of Facioscapulohumeral Muscular Dystrophy.
Lim, Kenji Rowel Q; Bittel, Adam; Maruyama, Rika; Echigoya, Yusuke; Nguyen, Quynh; Huang, Yiqing; Dzierlega, Kasia; Zhang, Aiping; Chen, Yi-Wen; Yokota, Toshifumi.
Afiliação
  • Lim KRQ; Department of Medical Genetics, Faculty of Medicine and Dentistry, University of Alberta, Edmonton, AB T6G2H7, Canada.
  • Bittel A; Center for Genetic Medicine Research, Children's National Health System, Washington, DC 20010, USA.
  • Maruyama R; Department of Medical Genetics, Faculty of Medicine and Dentistry, University of Alberta, Edmonton, AB T6G2H7, Canada.
  • Echigoya Y; Laboratory of Biomedical Science, Department of Veterinary Medicine, College of Bioresource Sciences, Nihon University, Fujisawa, Kanagawa 252-0880, Japan.
  • Nguyen Q; Department of Medical Genetics, Faculty of Medicine and Dentistry, University of Alberta, Edmonton, AB T6G2H7, Canada.
  • Huang Y; Department of Medical Genetics, Faculty of Medicine and Dentistry, University of Alberta, Edmonton, AB T6G2H7, Canada.
  • Dzierlega K; Department of Medical Genetics, Faculty of Medicine and Dentistry, University of Alberta, Edmonton, AB T6G2H7, Canada.
  • Zhang A; Center for Genetic Medicine Research, Children's National Health System, Washington, DC 20010, USA.
  • Chen YW; Center for Genetic Medicine Research, Children's National Health System, Washington, DC 20010, USA; Department of Genomics and Precision Medicine, School of Medicine and Health Science, George Washington University, Washington, DC 20052, USA. Electronic address: ychen@childrensnational.org.
  • Yokota T; Department of Medical Genetics, Faculty of Medicine and Dentistry, University of Alberta, Edmonton, AB T6G2H7, Canada; Muscular Dystrophy Canada Research Chair, Edmonton, AB T6G2H7, Canada. Electronic address: toshifumi.yokota@ualberta.ca.
Mol Ther ; 29(2): 848-858, 2021 02 03.
Article em En | MEDLINE | ID: mdl-33068777
Assuntos
Palavras-chave
Texto completo
Imprimir
XML
PubMed Links
Buscar no Google

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Terapia Genética / Oligonucleotídeos Antissenso / Proteínas de Homeodomínio / Distrofia Muscular Facioescapuloumeral / Inativação Gênica / Técnicas de Silenciamento de Genes Limite: Animals / Humans Idioma: En Revista: Mol Ther Assunto da revista: BIOLOGIA MOLECULAR / TERAPEUTICA Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Canadá
Texto completo
Imprimir
XML
PubMed Links
Buscar no Google

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Terapia Genética / Oligonucleotídeos Antissenso / Proteínas de Homeodomínio / Distrofia Muscular Facioescapuloumeral / Inativação Gênica / Técnicas de Silenciamento de Genes Limite: Animals / Humans Idioma: En Revista: Mol Ther Assunto da revista: BIOLOGIA MOLECULAR / TERAPEUTICA Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Canadá