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mTOR Inhibition with Sirolimus in Multiple System Atrophy: A Randomized, Double-Blind, Placebo-Controlled Futility Trial and 1-Year Biomarker Longitudinal Analysis.
Palma, Jose-Alberto; Martinez, Jose; Millar Vernetti, Patricio; Ma, Thong; Perez, Miguel A; Zhong, Judy; Qian, Yingzhi; Dutta, Suman; Maina, Katherine N; Siddique, Ibrar; Bitan, Gal; Ades-Aron, Benjamin; Shepherd, Timothy M; Kang, Un J; Kaufmann, Horacio.
Afiliação
  • Palma JA; Department of Neurology, New York University Grossman School of Medicine, New York, New York, USA.
  • Martinez J; Department of Neurology, New York University Grossman School of Medicine, New York, New York, USA.
  • Millar Vernetti P; Department of Neurology, New York University Grossman School of Medicine, New York, New York, USA.
  • Ma T; Department of Neurology, New York University Grossman School of Medicine, New York, New York, USA.
  • Perez MA; Department of Neurology, New York University Grossman School of Medicine, New York, New York, USA.
  • Zhong J; Department of Population Health, Division of Biostatistics, New York University Grossman School of Medicine, New York, New York, USA.
  • Qian Y; Department of Population Health, Division of Biostatistics, New York University Grossman School of Medicine, New York, New York, USA.
  • Dutta S; Department of Neurology, David Geffen School of Medicine, University of California Los Angeles, Los Angeles, California, USA.
  • Maina KN; Department of Neurology, David Geffen School of Medicine, University of California Los Angeles, Los Angeles, California, USA.
  • Siddique I; Department of Neurology, David Geffen School of Medicine, University of California Los Angeles, Los Angeles, California, USA.
  • Bitan G; Department of Neurology, David Geffen School of Medicine, University of California Los Angeles, Los Angeles, California, USA.
  • Ades-Aron B; Brain Research Institute, University of California, Los Angeles, California, USA.
  • Shepherd TM; Molecular Biology Institute, University of California, Los Angeles, California, USA.
  • Kang UJ; Department of Radiology, New York University Grossman School of Medicine, New York, New York, USA.
  • Kaufmann H; Department of Radiology, New York University Grossman School of Medicine, New York, New York, USA.
Mov Disord ; 37(4): 778-789, 2022 04.
Article em En | MEDLINE | ID: mdl-35040506

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Atrofia de Múltiplos Sistemas / Alfa-Sinucleína Tipo de estudo: Clinical_trials / Prognostic_studies / Risk_factors_studies Limite: Humans Idioma: En Revista: Mov Disord Assunto da revista: NEUROLOGIA Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Estados Unidos

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Atrofia de Múltiplos Sistemas / Alfa-Sinucleína Tipo de estudo: Clinical_trials / Prognostic_studies / Risk_factors_studies Limite: Humans Idioma: En Revista: Mov Disord Assunto da revista: NEUROLOGIA Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Estados Unidos