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ß-secretase 1 overexpression by AAV-mediated gene delivery prevents retina degeneration in a mouse model of age-related macular degeneration.
Qi, Xiaoping; Francelin, Carolina; Mitter, Sayak; Boye, Sanford L; Gu, Hongmei; Quigley, Judith; Grant, Maria B; Boulton, Michael E.
Afiliação
  • Qi X; Department of Ophthalmology and Visual Sciences, University of Alabama at Birmingham, Birmingham, AL 35294, USA.
  • Francelin C; Department of Ophthalmology and Visual Sciences, University of Alabama at Birmingham, Birmingham, AL 35294, USA.
  • Mitter S; Department of Ophthalmology and Visual Sciences, University of Alabama at Birmingham, Birmingham, AL 35294, USA.
  • Boye SL; MD-Powell Gene Therapy Center, University of Florida, Gainesville, FL 32611, USA.
  • Gu H; Department of Ophthalmology, Indiana University School of Medicine, Indianapolis, IN 46202, USA.
  • Quigley J; Department of Ophthalmology, Indiana University School of Medicine, Indianapolis, IN 46202, USA.
  • Grant MB; Department of Ophthalmology and Visual Sciences, University of Alabama at Birmingham, Birmingham, AL 35294, USA.
  • Boulton ME; Department of Ophthalmology and Visual Sciences, University of Alabama at Birmingham, Birmingham, AL 35294, USA. Electronic address: meboulton@uabmc.edu.
Mol Ther ; 31(7): 2042-2055, 2023 07 05.
Article em En | MEDLINE | ID: mdl-37016576

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Secretases da Proteína Precursora do Amiloide / Degeneração Macular Limite: Animals Idioma: En Revista: Mol Ther Assunto da revista: BIOLOGIA MOLECULAR / TERAPEUTICA Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Estados Unidos

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Secretases da Proteína Precursora do Amiloide / Degeneração Macular Limite: Animals Idioma: En Revista: Mol Ther Assunto da revista: BIOLOGIA MOLECULAR / TERAPEUTICA Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Estados Unidos