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Moving toward Individual Treatment Goals with Pegcetacoplan in Patients with PNH and Impaired Bone Marrow Function.
Szer, Jeff; Panse, Jens; Kulasekararaj, Austin; Oliver, Monika; Fattizzo, Bruno; Nishimura, Jun-Ichi; Horneff, Regina; Szamosi, Johan; Peffault de Latour, Régis.
Afiliação
  • Szer J; Department of Clinical Haematology, Peter MacCallum Cancer Centre, Royal Melbourne Hospital, Melbourne, VIC 3052, Australia.
  • Panse J; Department of Oncology, Hematology, Hemostaseology and Stem Cell Transplantation, University Hospital RWTH Aachen, 52074 Aachen, Germany.
  • Kulasekararaj A; Centre for Integrated Oncology (CIO) Aachen-Bonn-Cologne-Düsseldorf (ABCD), 52074 Aachen, Germany.
  • Oliver M; Department of Haematological Medicine, King's College Hospital, National Institute of Health Research/Wellcome King's Clinical Research Facility, London SE5 9RS, UK.
  • Fattizzo B; Division of Hemtatology, Department of Apheresis Medicine, University of Alberta Hospital, University of Alberta, Edmonton, AB T6G 2B7, Canada.
  • Nishimura JI; Hematology Unit, Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, 20122 Milan, Italy.
  • Horneff R; Department of Oncology and Hemato-Oncology, University of Milan, 20122 Milan, Italy.
  • Szamosi J; Department of Hematology and Oncology, Osaka University Graduate School of Medicine, Osaka 565-0871, Japan.
  • Peffault de Latour R; Swedish Orphan Biovitrum AB, 171 65 Stockholm, Sweden.
Int J Mol Sci ; 25(16)2024 Aug 06.
Article em En | MEDLINE | ID: mdl-39201278

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Medula Óssea / Hemoglobinúria Paroxística Limite: Adult / Aged / Female / Humans / Male / Middle aged Idioma: En Revista: Int J Mol Sci Ano de publicação: 2024 Tipo de documento: Article País de afiliação: Austrália

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Medula Óssea / Hemoglobinúria Paroxística Limite: Adult / Aged / Female / Humans / Male / Middle aged Idioma: En Revista: Int J Mol Sci Ano de publicação: 2024 Tipo de documento: Article País de afiliação: Austrália