1.
Clin Case Rep
; 12(8): e9312, 2024 Aug.
Artigo
em Inglês
| MEDLINE
| ID: mdl-39139619
RESUMO
Recommendations advise factor IX desensitization before immune tolerance induction in severe hemophilia B, supported by immunosuppression. A child with inhibitor and anaphylaxis to factor IX showed successful immunosuppression-free immune tolerance induction using very low and slowly increasing doses of a factor IX extended-half-life product. Immune tolerance to factor IX based on this protocol merits further study.