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Promoterless gene targeting without nucleases ameliorates haemophilia B in mice.
Barzel, A; Paulk, N K; Shi, Y; Huang, Y; Chu, K; Zhang, F; Valdmanis, P N; Spector, L P; Porteus, M H; Gaensler, K M; Kay, M A.
Afiliação
  • Barzel A; Departments of Pediatrics and Genetics, 269 Campus Drive, CCSR Building, Room 2105, Stanford, California 94305-5164, USA.
  • Paulk NK; Departments of Pediatrics and Genetics, 269 Campus Drive, CCSR Building, Room 2105, Stanford, California 94305-5164, USA.
  • Shi Y; Department of Medicine, Box 1270, UCSF, San Francisco, California 94143-1270, USA.
  • Huang Y; Departments of Pediatrics and Genetics, 269 Campus Drive, CCSR Building, Room 2105, Stanford, California 94305-5164, USA.
  • Chu K; Departments of Pediatrics and Genetics, 269 Campus Drive, CCSR Building, Room 2105, Stanford, California 94305-5164, USA.
  • Zhang F; Departments of Pediatrics and Genetics, 269 Campus Drive, CCSR Building, Room 2105, Stanford, California 94305-5164, USA.
  • Valdmanis PN; Departments of Pediatrics and Genetics, 269 Campus Drive, CCSR Building, Room 2105, Stanford, California 94305-5164, USA.
  • Spector LP; Departments of Pediatrics and Genetics, 269 Campus Drive, CCSR Building, Room 2105, Stanford, California 94305-5164, USA.
  • Porteus MH; Department of Pediatrics, 269 Campus Drive, Lorry Lokey Stem Cell Research Building, Room G3045, Stanford, California 94305-5164, USA.
  • Gaensler KM; Department of Medicine, Box 1270, UCSF, San Francisco, California 94143-1270, USA.
  • Kay MA; Departments of Pediatrics and Genetics, 269 Campus Drive, CCSR Building, Room 2105, Stanford, California 94305-5164, USA.
Nature ; 517(7534): 360-4, 2015 Jan 15.
Article em En | MEDLINE | ID: mdl-25363772

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Fator IX / Hemofilia B / Marcação de Genes Idioma: En Ano de publicação: 2015 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Fator IX / Hemofilia B / Marcação de Genes Idioma: En Ano de publicação: 2015 Tipo de documento: Article