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Gene Therapy of the ß-Hemoglobinopathies by Lentiviral Transfer of the ß(A(T87Q))-Globin Gene.
Negre, Olivier; Eggimann, Anne-Virginie; Beuzard, Yves; Ribeil, Jean-Antoine; Bourget, Philippe; Borwornpinyo, Suparerk; Hongeng, Suradej; Hacein-Bey, Salima; Cavazzana, Marina; Leboulch, Philippe; Payen, Emmanuel.
Afiliação
  • Negre O; 1 bluebird bio, Cambridge, Massachusetts.
  • Eggimann AV; 2 CEA, Institute of Emerging Disease and Innovative Therapies (iMETI) , Fontenay aux Roses, France .
  • Beuzard Y; 1 bluebird bio, Cambridge, Massachusetts.
  • Ribeil JA; 2 CEA, Institute of Emerging Disease and Innovative Therapies (iMETI) , Fontenay aux Roses, France .
  • Bourget P; 3 UMR 007, University of Paris 11 and CEA , CEA-iMETI, Fontenay aux Roses, France .
  • Borwornpinyo S; 4 Necker Hospital , Assistance Publique-Hôpitaux de Paris, Paris, France .
  • Hongeng S; 4 Necker Hospital , Assistance Publique-Hôpitaux de Paris, Paris, France .
  • Hacein-Bey S; 5 Mahidol University , Bangkok, Thailand .
  • Cavazzana M; 5 Mahidol University , Bangkok, Thailand .
  • Leboulch P; 6 Immunology Laboratory, Groupe Hospitalier Universitaire Paris-Sud , Assistance Publique-Hôpitaux de Paris, Paris, France .
  • Payen E; 4 Necker Hospital , Assistance Publique-Hôpitaux de Paris, Paris, France .
Hum Gene Ther ; 27(2): 148-65, 2016 Feb.
Article em En | MEDLINE | ID: mdl-26886832

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Terapia Genética / Talassemia beta / Transplante de Células-Tronco Hematopoéticas / Globinas beta / Anemia Falciforme Idioma: En Ano de publicação: 2016 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Terapia Genética / Talassemia beta / Transplante de Células-Tronco Hematopoéticas / Globinas beta / Anemia Falciforme Idioma: En Ano de publicação: 2016 Tipo de documento: Article