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Antisense pre-treatment increases gene therapy efficacy in dystrophic muscles.
Peccate, Cécile; Mollard, Amédée; Le Hir, Maëva; Julien, Laura; McClorey, Graham; Jarmin, Susan; Le Heron, Anita; Dickson, George; Benkhelifa-Ziyyat, Sofia; Piétri-Rouxel, France; Wood, Matthew J; Voit, Thomas; Lorain, Stéphanie.
Afiliação
  • Peccate C; Sorbonne Universités UPMC Univ Paris 06, Inserm, CNRS, Institut de Myologie, Centre de Recherche en Myologie (CRM), GH Pitié Salpêtrière, 105 bd de l'Hôpital, Paris 13, France.
  • Mollard A; Sorbonne Universités UPMC Univ Paris 06, Inserm, CNRS, Institut de Myologie, Centre de Recherche en Myologie (CRM), GH Pitié Salpêtrière, 105 bd de l'Hôpital, Paris 13, France.
  • Le Hir M; Université de Versailles St-Quentin, INSERM U1179, LIA BAHN CSM, Montigny-le-Bretonneux, France.
  • Julien L; Sorbonne Universités UPMC Univ Paris 06, Inserm, CNRS, Institut de Myologie, Centre de Recherche en Myologie (CRM), GH Pitié Salpêtrière, 105 bd de l'Hôpital, Paris 13, France.
  • McClorey G; Department of Physiology, Anatomy and Genetics, South Parks Road, Oxford, OX1 3QX, UK.
  • Jarmin S; School of Biological Sciences, Royal Holloway, University of London, Egham, Surrey, TW20 0EX, UK.
  • Le Heron A; School of Biological Sciences, Royal Holloway, University of London, Egham, Surrey, TW20 0EX, UK.
  • Dickson G; School of Biological Sciences, Royal Holloway, University of London, Egham, Surrey, TW20 0EX, UK.
  • Benkhelifa-Ziyyat S; Sorbonne Universités UPMC Univ Paris 06, Inserm, CNRS, Institut de Myologie, Centre de Recherche en Myologie (CRM), GH Pitié Salpêtrière, 105 bd de l'Hôpital, Paris 13, France.
  • Piétri-Rouxel F; Sorbonne Universités UPMC Univ Paris 06, Inserm, CNRS, Institut de Myologie, Centre de Recherche en Myologie (CRM), GH Pitié Salpêtrière, 105 bd de l'Hôpital, Paris 13, France.
  • Wood MJ; Department of Physiology, Anatomy and Genetics, South Parks Road, Oxford, OX1 3QX, UK.
  • Voit T; Sorbonne Universités UPMC Univ Paris 06, Inserm, CNRS, Institut de Myologie, Centre de Recherche en Myologie (CRM), GH Pitié Salpêtrière, 105 bd de l'Hôpital, Paris 13, France.
  • Lorain S; NIHR Biomedical Research Centre, Institute of Child Health, University College London, 30 Guilford Street, London, WC1N 1EH, UK.
Hum Mol Genet ; 25(16): 3555-3563, 2016 08 15.
Article em En | MEDLINE | ID: mdl-27378686

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Terapia Genética / Distrofina / Oligonucleotídeos Antissenso / Distrofia Muscular de Duchenne / Morfolinos / Distrofia Muscular Animal Idioma: En Ano de publicação: 2016 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Terapia Genética / Distrofina / Oligonucleotídeos Antissenso / Distrofia Muscular de Duchenne / Morfolinos / Distrofia Muscular Animal Idioma: En Ano de publicação: 2016 Tipo de documento: Article