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Adeno Associated Virus 9-Based Gene Therapy Delivers a Functional Monocarboxylate Transporter 8, Improving Thyroid Hormone Availability to the Brain of Mct8-Deficient Mice.
Iwayama, Hideyuki; Liao, Xiao-Hui; Braun, Lyndsey; Bárez-López, Soledad; Kaspar, Brian; Weiss, Roy E; Dumitrescu, Alexandra M; Guadaño-Ferraz, Ana; Refetoff, Samuel.
Afiliação
  • Iwayama H; 1 Department of Medicine, The University of Chicago , Chicago, Illinois.
  • Liao XH; 1 Department of Medicine, The University of Chicago , Chicago, Illinois.
  • Braun L; 2 Research Institute at Nationwide Children's Hospital , Columbus, Ohio.
  • Bárez-López S; 3 Department of Neuroscience, The Ohio State University , Columbus, Ohio.
  • Kaspar B; 4 Institute for Biomedical Research "Alberto Sols," Consejo Superior de Investigaciones Científicas-Universidad Autónoma de Madrid , Madrid, Spain .
  • Weiss RE; 5 Center for Biomedical Research on Rare Diseases (Ciberer), Instituto de Salud Carlos III , Madrid, Spain .
  • Dumitrescu AM; 2 Research Institute at Nationwide Children's Hospital , Columbus, Ohio.
  • Guadaño-Ferraz A; 3 Department of Neuroscience, The Ohio State University , Columbus, Ohio.
  • Refetoff S; 6 Department of Medicine, University of Miami , Miami, Florida.
Thyroid ; 26(9): 1311-9, 2016 09.
Article em En | MEDLINE | ID: mdl-27432638

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Proteínas de Membrana Transportadoras / Hormônios Tireóideos / Encéfalo Idioma: En Ano de publicação: 2016 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Proteínas de Membrana Transportadoras / Hormônios Tireóideos / Encéfalo Idioma: En Ano de publicação: 2016 Tipo de documento: Article