Correction of Monogenic and Common Retinal Disorders with Gene Therapy.

Sengillo, Jesse D; Justus, Sally; Cabral, Thiago; Tsang, Stephen H.

Afiliação

Sengillo JD; Jonas Children's Vision Care, and Bernard & Shirlee Brown Glaucoma Laboratory, Department of Ophthalmology, Columbia University Medical Center, New York, NY, 10032 USA. js3899@cumc.columbia.edu.
Justus S; Edward S. Harkness Eye Institute, New York-Presbyterian Hospital, New York, NY, 10032 USA. js3899@cumc.columbia.edu.
Cabral T; State University of New York Downstate Medical Center, Brooklyn, NY, 11203 USA. js3899@cumc.columbia.edu.
Tsang SH; Jonas Children's Vision Care, and Bernard & Shirlee Brown Glaucoma Laboratory, Department of Ophthalmology, Columbia University Medical Center, New York, NY, 10032 USA. sj2750@cumc.columbia.edu.

Genes (Basel) ; 8(2)2017 Jan 27.

Article em En | MEDLINE | ID: mdl-28134823

Palavras-chave

gene therapy, genome engineering, CRISPR, retinal degeneration, inherited retinal disease

Texto completo: 1 Base de dados: MEDLINE Idioma: En Ano de publicação: 2017 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Idioma: En Ano de publicação: 2017 Tipo de documento: Article