Improved <i>MECP2</i> Gene Therapy Extends the Survival of MeCP2-Null Mice without Apparent Toxicity after Intracisternal Delivery.

Sinnett, Sarah E; Hector, Ralph D; Gadalla, Kamal K E; Heindel, Clifford; Chen, Daphne; Zaric, Violeta; Bailey, Mark E S; Cobb, Stuart R; Gray, Steven J

Improved MECP2 Gene Therapy Extends the Survival of MeCP2-Null Mice without Apparent Toxicity after Intracisternal Delivery.

Sinnett, Sarah E; Hector, Ralph D; Gadalla, Kamal K E; Heindel, Clifford; Chen, Daphne; Zaric, Violeta; Bailey, Mark E S; Cobb, Stuart R; Gray, Steven J.

Afiliação

Sinnett SE; University of North Carolina (UNC) Gene Therapy Center, Chapel Hill, NC 27599, USA.
Hector RD; Carolina Institute for Developmental Disabilities, Chapel Hill, NC 27510, USA.
Gadalla KKE; Institute of Neuroscience and Psychology, University of Glasgow, Glasgow G12 8QQ, UK.
Heindel C; Institute of Neuroscience and Psychology, University of Glasgow, Glasgow G12 8QQ, UK.
Chen D; Pharmacology Department, Faculty of Medicine, Tanta University, Tanta 31111, Egypt.
Zaric V; University of North Carolina (UNC) Gene Therapy Center, Chapel Hill, NC 27599, USA.
Bailey MES; University of North Carolina (UNC) Gene Therapy Center, Chapel Hill, NC 27599, USA.
Cobb SR; University of North Carolina (UNC) Gene Therapy Center, Chapel Hill, NC 27599, USA.
Gray SJ; School of Life Sciences, College of Medical, Veterinary and Life Sciences, University of Glasgow, Glasgow G12 8QQ, UK.