Evaluation of Antisense Oligonucleotides Targeting ATXN3 in SCA3 Mouse Models.

Moore, Lauren R; Rajpal, Gautam; Dillingham, Ian T; Qutob, Maya; Blumenstein, Kate G; Gattis, Danielle; Hung, Gene; Kordasiewicz, Holly B; Paulson, Henry L; McLoughlin, Hayley S.

Afiliação

Moore LR; Department of Neurology, University of Michigan, Ann Arbor, MI 48109-2200, USA.
Rajpal G; Department of Neurology, University of Michigan, Ann Arbor, MI 48109-2200, USA.
Dillingham IT; Department of Neurology, University of Michigan, Ann Arbor, MI 48109-2200, USA.
Qutob M; Department of Neurology, University of Michigan, Ann Arbor, MI 48109-2200, USA.
Blumenstein KG; Department of Neurology, University of Michigan, Ann Arbor, MI 48109-2200, USA.
Gattis D; Ionis Pharmaceuticals, Carlsbad, CA 92008, USA.
Hung G; Ionis Pharmaceuticals, Carlsbad, CA 92008, USA.
Kordasiewicz HB; Ionis Pharmaceuticals, Carlsbad, CA 92008, USA.
Paulson HL; Department of Neurology, University of Michigan, Ann Arbor, MI 48109-2200, USA. Electronic address: henryp@umich.edu.
McLoughlin HS; Department of Neurology, University of Michigan, Ann Arbor, MI 48109-2200, USA. Electronic address: hayleymc@umich.edu.