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Preclinical studies for a phase 1 clinical trial of autologous hematopoietic stem cell gene therapy for sickle cell disease.
Urbinati, Fabrizia; Wherley, Jennifer; Geiger, Sabine; Fernandez, Beatriz Campo; Kaufman, Michael L; Cooper, Aaron; Romero, Zulema; Marchioni, Filippo; Reeves, Lilith; Read, Elizabeth; Nowicki, Barbara; Grassman, Elke; Viswanathan, Shivkumar; Wang, Xiaoyan; Hollis, Roger P; Kohn, Donald B.
Afiliação
  • Urbinati F; Department of Microbiology, Immunology and Molecular Genetics and the Eli & Edythe Broad Stem Cell Research Center, University of California, Los Angeles, California, USA.
  • Wherley J; Department of Microbiology, Immunology and Molecular Genetics and the Eli & Edythe Broad Stem Cell Research Center, University of California, Los Angeles, California, USA.
  • Geiger S; Department of Microbiology, Immunology and Molecular Genetics and the Eli & Edythe Broad Stem Cell Research Center, University of California, Los Angeles, California, USA.
  • Fernandez BC; Department of Microbiology, Immunology and Molecular Genetics and the Eli & Edythe Broad Stem Cell Research Center, University of California, Los Angeles, California, USA.
  • Kaufman ML; Department of Microbiology, Immunology and Molecular Genetics and the Eli & Edythe Broad Stem Cell Research Center, University of California, Los Angeles, California, USA.
  • Cooper A; Department of Microbiology, Immunology and Molecular Genetics and the Eli & Edythe Broad Stem Cell Research Center, University of California, Los Angeles, California, USA.
  • Romero Z; Department of Microbiology, Immunology and Molecular Genetics and the Eli & Edythe Broad Stem Cell Research Center, University of California, Los Angeles, California, USA.
  • Marchioni F; Department of Microbiology, Immunology and Molecular Genetics and the Eli & Edythe Broad Stem Cell Research Center, University of California, Los Angeles, California, USA.
  • Reeves L; Translational Core Laboratory, Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, USA.
  • Read E; Consultant, San Francisco, California, USA.
  • Nowicki B; UCLA BM/Stem Cell Transplant Laboratory, University of California, Los Angeles, USA.
  • Grassman E; Translational Trials Development and Support Labs, Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, USA.
  • Viswanathan S; Translational Trials Development and Support Labs, Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, USA.
  • Wang X; Department of General Internal Medicine and Health Services Research, University of California, Los Angeles, USA.
  • Hollis RP; Department of Microbiology, Immunology and Molecular Genetics and the Eli & Edythe Broad Stem Cell Research Center, University of California, Los Angeles, California, USA.
  • Kohn DB; Department of Microbiology, Immunology and Molecular Genetics and the Eli & Edythe Broad Stem Cell Research Center, University of California, Los Angeles, California, USA. Electronic address: e-dkohn@mednet.ucla.edu.
Cytotherapy ; 19(9): 1096-1112, 2017 09.
Article em En | MEDLINE | ID: mdl-28733131

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Células-Tronco Hematopoéticas / Terapia Genética / Transplante de Células-Tronco Hematopoéticas / Anemia Falciforme Idioma: En Ano de publicação: 2017 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Células-Tronco Hematopoéticas / Terapia Genética / Transplante de Células-Tronco Hematopoéticas / Anemia Falciforme Idioma: En Ano de publicação: 2017 Tipo de documento: Article