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Relationship Between Glucocerebrosidase Activity and Clinical Response to Enzyme Replacement Therapy in Patients With Gaucher Disease Type I.
Gras-Colomer, Elena; Martínez-Gómez, María-Amparo; Climente-Martí, Mónica; Fernandez-Zarzoso, Miguel; Almela-Tejedo, Mercedes; Giner-Galvañ, Vicente; Marcos-Rodríguez, Jose-Antonio; Rodríguez-Fernández, Alicia; Torralba-Cabeza, Miguel-Ángel; Merino-Sanjuan, Matilde.
Afiliação
  • Gras-Colomer E; Department of Pharmacy, University Hospital Doctor Peset of Valencia, Valencia, Spain.
  • Martínez-Gómez MA; Foundation for the Promotion of Health and Biomedical Research of Valencia (FISABIO), Valencia, Spain.
  • Climente-Martí M; Department of Pharmacy, University Hospital Doctor Peset of Valencia, Valencia, Spain.
  • Fernandez-Zarzoso M; Foundation for the Promotion of Health and Biomedical Research of Valencia (FISABIO), Valencia, Spain.
  • Almela-Tejedo M; Department of Pharmacy, University Hospital Doctor Peset of Valencia, Valencia, Spain.
  • Giner-Galvañ V; Pharmacy and Pharmaceutical Technology, University of Valencia, Valencia, Spain.
  • Marcos-Rodríguez JA; Department of Hematology, University Hospital Doctor Peset of Valencia, Valencia, Spain.
  • Rodríguez-Fernández A; Department of Pharmacy, Hospital Virgen de los Lirios of Alcoi, Alcoi, Spain.
  • Torralba-Cabeza MÁ; Department of Internal Medicine, Hospital Virgen de los Lirios of Alcoi, Alcoi, Spain.
  • Merino-Sanjuan M; Department of Pharmacy, University Hospital Virgen Macarena, Seville, Spain.
Basic Clin Pharmacol Toxicol ; 123(1): 65-71, 2018 Jul.
Article em En | MEDLINE | ID: mdl-29418074

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Terapia de Reposição de Enzimas / Doença de Gaucher / Glucosilceramidase / Leucócitos Idioma: En Ano de publicação: 2018 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Terapia de Reposição de Enzimas / Doença de Gaucher / Glucosilceramidase / Leucócitos Idioma: En Ano de publicação: 2018 Tipo de documento: Article