Replacement Therapies in Metabolic Disease.

Keller, Alexander S; Keller Iv, T C Stevenson; DeLalio, Leon J; Shahab, Guleer; Yang, Yang; Murphy, Sara A; Shu, Xiaohong; Isakson, Brant E

Keller, Alexander S; Keller Iv, T C Stevenson; DeLalio, Leon J; Shahab, Guleer; Yang, Yang; Murphy, Sara A; Shu, Xiaohong; Isakson, Brant E.

Afiliação

Keller AS; Robert M. Berne Cardiovascular Research Center, University of Virginia, Charlottesville, Virginia, United States.
Keller Iv TCS; Department of Pharmacology, University of Virginia, Charlottesville, Virginia, United States.
DeLalio LJ; Robert M. Berne Cardiovascular Research Center, University of Virginia, Charlottesville, Virginia, United States.
Shahab G; Department of Molecular Physiology and Biological Physics, University of Virginia, Charlottesville, Virginia, United States.
Yang Y; Robert M. Berne Cardiovascular Research Center, University of Virginia, Charlottesville, Virginia, United States.
Murphy SA; Department of Pharmacology, University of Virginia, Charlottesville, Virginia, United States.
Shu X; Robert M. Berne Cardiovascular Research Center, University of Virginia, Charlottesville, Virginia, United States.
Isakson BE; College of Pharmacy, Dalian Medical University, Dalian, Liaoning, China.

Curr Pharm Biotechnol ; 19(5): 382-399, 2018.

Article em En | MEDLINE | ID: mdl-29921204

Assuntos

Terapia de Reposição de Enzimas/métodos; Doenças Metabólicas/terapia; Terapia Genética; Humanos; Doenças por Armazenamento dos Lisossomos/terapia

Palavras-chave

Rare diseases; enzyme replacement therapy; gene therapy; lysosomal storage disorder; metabolic disease; recombinant enzymes.

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Texto completo: 1 Base de dados: MEDLINE Assunto principal: Terapia de Reposição de Enzimas / Doenças Metabólicas Idioma: En Ano de publicação: 2018 Tipo de documento: Article

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