Your browser doesn't support javascript.
loading
Systemic messenger RNA as an etiological treatment for acute intermittent porphyria.
Jiang, Lei; Berraondo, Pedro; Jericó, Daniel; Guey, Lin T; Sampedro, Ana; Frassetto, Andrea; Benenato, Kerry E; Burke, Kristine; Santamaría, Eva; Alegre, Manuel; Pejenaute, Álvaro; Kalariya, Mayur; Butcher, William; Park, Ji-Sun; Zhu, Xuling; Sabnis, Staci; Kumarasinghe, E Sathyajith; Salerno, Timothy; Kenney, Matthew; Lukacs, Christine M; Ávila, Matías A; Martini, Paolo G V; Fontanellas, Antonio.
Afiliação
  • Jiang L; Moderna Therapeutics, Cambridge, MA, USA.
  • Berraondo P; Program of Immunology and Immunotherapy, Centre for Applied Medical Research (CIMA), University of Navarra, Pamplona, Spain.
  • Jericó D; Instituto de Investigación Sanitaria de Navarra (IdiSNA), Pamplona, Spain.
  • Guey LT; Centro de Investigación Biomédica en Red de Cáncer (CIBERONC), Instituto de Salud Carlos III, Madrid, Spain.
  • Sampedro A; Instituto de Investigación Sanitaria de Navarra (IdiSNA), Pamplona, Spain.
  • Frassetto A; Hepatology Program, Centre for Applied Medical Research (CIMA), University of Navarra, Pamplona, Spain.
  • Benenato KE; Moderna Therapeutics, Cambridge, MA, USA.
  • Burke K; Instituto de Investigación Sanitaria de Navarra (IdiSNA), Pamplona, Spain.
  • Santamaría E; Hepatology Program, Centre for Applied Medical Research (CIMA), University of Navarra, Pamplona, Spain.
  • Alegre M; Moderna Therapeutics, Cambridge, MA, USA.
  • Pejenaute Á; Moderna Therapeutics, Cambridge, MA, USA.
  • Kalariya M; Moderna Therapeutics, Cambridge, MA, USA.
  • Butcher W; Instituto de Investigación Sanitaria de Navarra (IdiSNA), Pamplona, Spain.
  • Park JS; Hepatology Program, Centre for Applied Medical Research (CIMA), University of Navarra, Pamplona, Spain.
  • Zhu X; Centro de Investigación Biomédica en Red de Enfermedades Hepáticas y Digestivas (CIBEREHD), Instituto de Salud Carlos III, Madrid, Spain.
  • Sabnis S; Department of Clinical Neurophysiology, Clínica Universitaria, University of Navarra, Pamplona, Spain.
  • Kumarasinghe ES; Neurophysiology Laboratory, Neuroscience Program, Centre for Applied Medical Research (CIMA), University of Navarra, Pamplona, Spain.
  • Salerno T; Department of Biochemistry and Genetics, University of Navarra, Pamplona, Spain.
  • Kenney M; Moderna Therapeutics, Cambridge, MA, USA.
  • Lukacs CM; Moderna Therapeutics, Cambridge, MA, USA.
  • Ávila MA; Moderna Therapeutics, Cambridge, MA, USA.
  • Martini PGV; Moderna Therapeutics, Cambridge, MA, USA.
  • Fontanellas A; Moderna Therapeutics, Cambridge, MA, USA.
Nat Med ; 24(12): 1899-1909, 2018 12.
Article em En | MEDLINE | ID: mdl-30297912
Assuntos
Texto completo
Imprimir
XML
PubMed Links
Buscar no Google

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Hidroximetilbilano Sintase / RNA Mensageiro / Terapia Genética / Porfiria Aguda Intermitente Idioma: En Ano de publicação: 2018 Tipo de documento: Article
Texto completo
Imprimir
XML
PubMed Links
Buscar no Google

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Hidroximetilbilano Sintase / RNA Mensageiro / Terapia Genética / Porfiria Aguda Intermitente Idioma: En Ano de publicação: 2018 Tipo de documento: Article