In-Depth Characterization of a Mifepristone-Regulated Expression System for AAV5-Mediated Gene Therapy in the Liver.

Liefhebber, Jolanda M; Martier, Raygene; Van der Zon, Tom; Keskin, Sonay; Huseinovic, Angelina; Lubelski, Jacek; Blits, Bas; Petry, Harald; Konstantinova, Pavlina

Liefhebber, Jolanda M; Martier, Raygene; Van der Zon, Tom; Keskin, Sonay; Huseinovic, Angelina; Lubelski, Jacek; Blits, Bas; Petry, Harald; Konstantinova, Pavlina.

Afiliação

Liefhebber JM; Department of Research & Development, uniQure N.V., 1105BP Amsterdam, the Netherlands.
Martier R; Department of Research & Development, uniQure N.V., 1105BP Amsterdam, the Netherlands.
Van der Zon T; Department of Gastroenterology and Hepatology, Leiden University Medical Center, Leiden, the Netherlands.
Keskin S; Department of Research & Development, uniQure N.V., 1105BP Amsterdam, the Netherlands.
Huseinovic A; Department of Research & Development, uniQure N.V., 1105BP Amsterdam, the Netherlands.
Lubelski J; Department of Research & Development, uniQure N.V., 1105BP Amsterdam, the Netherlands.
Blits B; Amsterdam UMC, the Netherlands.
Petry H; Department of Research & Development, uniQure N.V., 1105BP Amsterdam, the Netherlands.
Konstantinova P; Department of Research & Development, uniQure N.V., 1105BP Amsterdam, the Netherlands.