Targeted exon skipping with AAV-mediated split adenine base editors.

Winter, Jackson; Luu, Alan; Gapinske, Michael; Manandhar, Sony; Shirguppe, Shraddha; Woods, Wendy S; Song, Jun S; Perez-Pinera, Pablo.

Afiliação

Winter J; 1Department of Bioengineering, University of Illinois at Urbana-Champaign, Urbana, IL 61801 USA.
Luu A; 2Department of Physics, University of Illinois at Urbana-Champaign, Urbana, IL 61801 USA.
Gapinske M; 3Carl R. Woese Institute for Genomic Biology, University of Illinois at Urbana-Champaign, Urbana, IL 61801 USA.
Manandhar S; 1Department of Bioengineering, University of Illinois at Urbana-Champaign, Urbana, IL 61801 USA.
Shirguppe S; 1Department of Bioengineering, University of Illinois at Urbana-Champaign, Urbana, IL 61801 USA.
Woods WS; 1Department of Bioengineering, University of Illinois at Urbana-Champaign, Urbana, IL 61801 USA.
Song JS; 1Department of Bioengineering, University of Illinois at Urbana-Champaign, Urbana, IL 61801 USA.
Perez-Pinera P; 2Department of Physics, University of Illinois at Urbana-Champaign, Urbana, IL 61801 USA.

Cell Discov ; 5: 41, 2019.

Article em En | MEDLINE | ID: mdl-31636954