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Effective and Accurate Gene Silencing by a Recombinant AAV-Compatible MicroRNA Scaffold.
Xie, Jun; Tai, Phillip W L; Brown, Alexander; Gong, Shoufang; Zhu, Sha; Wang, Yi; Li, Chengjian; Colpan, Cansu; Su, Qin; He, Ran; Ma, Hong; Li, Jia; Ye, Hanqing; Ko, Jihye; Zamore, Phillip D; Gao, Guangping.
Afiliação
  • Xie J; Horae Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA, USA; Viral Vector Core, University of Massachusetts Medical School, Worcester, MA, USA; Li Weibo Institute for Rare Diseases Research, University of Massachusetts Medical School, Worcester, MA, USA; Department of M
  • Tai PWL; Horae Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA, USA; Li Weibo Institute for Rare Diseases Research, University of Massachusetts Medical School, Worcester, MA, USA; Department of Microbiology and Physiological Systems, University of Massachusetts Medical School,
  • Brown A; Horae Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA, USA; Li Weibo Institute for Rare Diseases Research, University of Massachusetts Medical School, Worcester, MA, USA; Department of Microbiology and Physiological Systems, University of Massachusetts Medical School,
  • Gong S; Horae Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA, USA; Li Weibo Institute for Rare Diseases Research, University of Massachusetts Medical School, Worcester, MA, USA; Department of Microbiology and Physiological Systems, University of Massachusetts Medical School,
  • Zhu S; Horae Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA, USA; Li Weibo Institute for Rare Diseases Research, University of Massachusetts Medical School, Worcester, MA, USA; Department of Microbiology and Physiological Systems, University of Massachusetts Medical School,
  • Wang Y; Horae Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA, USA; Li Weibo Institute for Rare Diseases Research, University of Massachusetts Medical School, Worcester, MA, USA; Department of Microbiology and Physiological Systems, University of Massachusetts Medical School,
  • Li C; Fornax Biotech, Worcester, MA, USA.
  • Colpan C; RNA Therapeutics Institute and Howard Hughes Medical Institute, University of Massachusetts Medical School, Worcester, MA, USA.
  • Su Q; Horae Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA, USA; Viral Vector Core, University of Massachusetts Medical School, Worcester, MA, USA; Li Weibo Institute for Rare Diseases Research, University of Massachusetts Medical School, Worcester, MA, USA.
  • He R; Horae Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA, USA; Viral Vector Core, University of Massachusetts Medical School, Worcester, MA, USA; Li Weibo Institute for Rare Diseases Research, University of Massachusetts Medical School, Worcester, MA, USA.
  • Ma H; Horae Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA, USA; Viral Vector Core, University of Massachusetts Medical School, Worcester, MA, USA; Li Weibo Institute for Rare Diseases Research, University of Massachusetts Medical School, Worcester, MA, USA.
  • Li J; Horae Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA, USA; Li Weibo Institute for Rare Diseases Research, University of Massachusetts Medical School, Worcester, MA, USA; Department of Microbiology and Physiological Systems, University of Massachusetts Medical School,
  • Ye H; Horae Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA, USA; Li Weibo Institute for Rare Diseases Research, University of Massachusetts Medical School, Worcester, MA, USA; Department of Microbiology and Physiological Systems, University of Massachusetts Medical School,
  • Ko J; Horae Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA, USA; Viral Vector Core, University of Massachusetts Medical School, Worcester, MA, USA; Li Weibo Institute for Rare Diseases Research, University of Massachusetts Medical School, Worcester, MA, USA.
  • Zamore PD; RNA Therapeutics Institute and Howard Hughes Medical Institute, University of Massachusetts Medical School, Worcester, MA, USA. Electronic address: phillip.zamore@umassmed.edu.
  • Gao G; Horae Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA, USA; Viral Vector Core, University of Massachusetts Medical School, Worcester, MA, USA; Li Weibo Institute for Rare Diseases Research, University of Massachusetts Medical School, Worcester, MA, USA; Department of M
Mol Ther ; 28(2): 422-430, 2020 02 05.
Article em En | MEDLINE | ID: mdl-31843447

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Dependovirus / Inativação Gênica / MicroRNAs / Vetores Genéticos Idioma: En Ano de publicação: 2020 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Dependovirus / Inativação Gênica / MicroRNAs / Vetores Genéticos Idioma: En Ano de publicação: 2020 Tipo de documento: Article