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Cardiomyopathy and kidney function in agalsidase beta-treated female Fabry patients: a pre-treatment vs. post-treatment analysis.
Wanner, Christoph; Feldt-Rasmussen, Ulla; Jovanovic, Ana; Linhart, Ales; Yang, Meng; Ponce, Elvira; Brand, Eva; Germain, Dominique P; Hughes, Derralynn A; Jefferies, John L; Martins, Ana Maria; Nowak, Albina; Vujkovac, Bojan; Weidemann, Frank; West, Michael L; Ortiz, Alberto.
Afiliação
  • Wanner C; Department of Medicine, Division of Nephrology, University Hospital Würzburg, Würzburg, Germany.
  • Feldt-Rasmussen U; Department of Medical Endocrinology, Rigshospitalet, Copenhagen University Hospital, Copenhagen, Denmark.
  • Jovanovic A; The Mark Holland Unit, Department of Endocrinology and Metabolic Medicine, Salford Royal NHS Foundation Trust, Salford, UK.
  • Linhart A; 2nd Department of Medicine, Department of Cardiovascular Medicine, First Faculty of Medicine, Charles University, General University Hospital, Prague, Czech Republic.
  • Yang M; Epidemiology & Biostatistics, Sanofi Genzyme, Cambridge, MA, USA.
  • Ponce E; Global Medical Affairs Rare Diseases, Sanofi Genzyme, Cambridge, MA, USA.
  • Brand E; Internal Medicine D, Department of Nephrology, Hypertension and Rheumatology, University Hospital Münster, Münster, Germany.
  • Germain DP; French Referral Center for Fabry Disease, Division of Medical Genetics and INSERM U1179, University of Versailles, Paris-Saclay University, Montigny, France.
  • Hughes DA; Lysosomal Storage Disorder Unit, Royal Free London NHS Foundation Trust and, University College London, London, UK.
  • Jefferies JL; Department of Medicine, Division of Cardiovascular Diseases, University of Tennessee Health Science Center, Memphis, TN, USA.
  • Martins AM; Department of Paediatrics, Federal University of São Paulo, São Paulo, Brazil.
  • Nowak A; Department of Internal Medicine, University Hospital of Zürich, University of Zürich, Zürich, Switzerland.
  • Vujkovac B; Department of Internal Medicine, General Hospital Slovenj Gradec, Slovenj Gradec, Slovenia.
  • Weidemann F; Medical Clinic I, Klinikum Vest, Knappschaftskrankenhaus, Recklinghausen, Germany.
  • West ML; Department of Medicine, Division of Nephrology, Dalhousie University, Halifax, Nova Scotia, Canada.
  • Ortiz A; Unidad de Dialisis, IIS-Fundación Jiménez Díaz, UAM, IRSIN, REDINREN, Madrid, Spain.
ESC Heart Fail ; 7(3): 825-834, 2020 06.
Article em En | MEDLINE | ID: mdl-32100468

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Doença de Fabry / Cardiomiopatias Idioma: En Ano de publicação: 2020 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Doença de Fabry / Cardiomiopatias Idioma: En Ano de publicação: 2020 Tipo de documento: Article