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TALEN mediated gene editing in a mouse model of Fanconi anemia.
Pino-Barrio, Maria José; Giménez, Yari; Villanueva, Mariela; Hildenbeutel, Marcus; Sánchez-Dominguez, Rebeca; Rodríguez-Perales, Sandra; Pujol, Roser; Surrallés, Jordi; Río, Paula; Cathomen, Toni; Mussolino, Claudio; Bueren, Juan Antonio; Navarro, Susana.
Afiliação
  • Pino-Barrio MJ; Division of Hematopoietic Innovative Therapies, CIEMAT/CIBERER, 28040, Madrid, Spain.
  • Giménez Y; Advanced Therapies Unit, IIS-Fundación Jimenez Diaz (IIS-FJD, UAM), 28040, Madrid, Spain.
  • Villanueva M; Center for Biomedical Network Research on Rare Diseases, Instituto de Salud Carlos III, Madrid, Spain.
  • Hildenbeutel M; Division of Hematopoietic Innovative Therapies, CIEMAT/CIBERER, 28040, Madrid, Spain.
  • Sánchez-Dominguez R; Advanced Therapies Unit, IIS-Fundación Jimenez Diaz (IIS-FJD, UAM), 28040, Madrid, Spain.
  • Rodríguez-Perales S; Center for Biomedical Network Research on Rare Diseases, Instituto de Salud Carlos III, Madrid, Spain.
  • Pujol R; Division of Hematopoietic Innovative Therapies, CIEMAT/CIBERER, 28040, Madrid, Spain.
  • Surrallés J; Advanced Therapies Unit, IIS-Fundación Jimenez Diaz (IIS-FJD, UAM), 28040, Madrid, Spain.
  • Río P; Center for Biomedical Network Research on Rare Diseases, Instituto de Salud Carlos III, Madrid, Spain.
  • Cathomen T; Institute for Transfusion Medicine and Gene Therapy, Medical Center - University of Freiburg, 79106, Freiburg, Germany.
  • Mussolino C; Center for Chronic Immunodeficiency, Medical Center - University of Freiburg, 79106, Freiburg, Germany.
  • Bueren JA; Division of Hematopoietic Innovative Therapies, CIEMAT/CIBERER, 28040, Madrid, Spain.
  • Navarro S; Advanced Therapies Unit, IIS-Fundación Jimenez Diaz (IIS-FJD, UAM), 28040, Madrid, Spain.
Sci Rep ; 10(1): 6997, 2020 04 24.
Article em En | MEDLINE | ID: mdl-32332829

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Anemia de Fanconi / Nucleases dos Efetores Semelhantes a Ativadores de Transcrição / Edição de Genes Idioma: En Ano de publicação: 2020 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Anemia de Fanconi / Nucleases dos Efetores Semelhantes a Ativadores de Transcrição / Edição de Genes Idioma: En Ano de publicação: 2020 Tipo de documento: Article