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In vitro assay for the efficacy assessment of AAV vectors expressing microdystrophin.
Danilov, Kirill A; Vassilieva, Svetlana G; Polikarpova, Anna V; Starikova, Anna V; Shmidt, Anna A; Galkin, Ivan I; Tsitrina, Alexandra A; Egorova, Tatiana V; Orlov, Sergei N; Kotelevtsev, Yuri V.
Afiliação
  • Danilov KA; Center of Life Sciences, Skolkovo Institute of Science and Technology, Moscow, 121205, Russia; Atlas Biomed Group Limited, Tintagel House, 92 Albert Embankment, Lambeth, SE1 7TY, London, United Kingdom. Electronic address: kirill.danilov@skoltech.ru.
  • Vassilieva SG; Laboratory of Modeling and Gene Therapy of Hereditary Diseases, Institute of Gene Biology, Russian Academy of Sciences, Moscow, 119334, Russia; Marlin Biotech LLC, Moscow, 143026, Russia. Electronic address: vassilievasvetlana@gmail.com.
  • Polikarpova AV; Laboratory of Modeling and Gene Therapy of Hereditary Diseases, Institute of Gene Biology, Russian Academy of Sciences, Moscow, 119334, Russia; Marlin Biotech LLC, Moscow, 143026, Russia. Electronic address: a.polikarpova.marlin@gmail.com.
  • Starikova AV; Laboratory of Modeling and Gene Therapy of Hereditary Diseases, Institute of Gene Biology, Russian Academy of Sciences, Moscow, 119334, Russia; Marlin Biotech LLC, Moscow, 143026, Russia. Electronic address: a.alexandrova.marlin@gmail.com.
  • Shmidt AA; Laboratory of Modeling and Gene Therapy of Hereditary Diseases, Institute of Gene Biology, Russian Academy of Sciences, Moscow, 119334, Russia; Marlin Biotech LLC, Moscow, 143026, Russia; Center for Precision Genome Editing and Genetic Technologies for Biomedicine, Institute of Gene Biology, Russian
  • Galkin II; Marlin Biotech LLC, Moscow, 143026, Russia; A.N. Belozersky Institute of Physico-Chemical Biology, Lomonosov Moscow State University, 119992, Moscow, Russia. Electronic address: i.galkin.marlin@gmail.com.
  • Tsitrina AA; Institute of Developmental Biology, Russian Academy of Sciences, Moscow, 119334, Russia. Electronic address: sapronova.a@idbras.ru.
  • Egorova TV; Laboratory of Modeling and Gene Therapy of Hereditary Diseases, Institute of Gene Biology, Russian Academy of Sciences, Moscow, 119334, Russia; Marlin Biotech LLC, Moscow, 143026, Russia. Electronic address: dimitrieva.ta@gmail.com.
  • Orlov SN; M.V. Lomonosov Moscow State University, Moscow, 119234, Russia; National Research Tomsk State University, Tomsk, 634050, Russia. Electronic address: sergeinorlov@yandex.ru.
  • Kotelevtsev YV; Center for Neurobiology and Brain Restoration, Skolkovo Institute of Science and Technology, Moscow, 121205, Russia. Electronic address: y.kotelevtsev@skoltech.ru.
Exp Cell Res ; 392(2): 112033, 2020 07 15.
Article em En | MEDLINE | ID: mdl-32360435

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Terapia Genética / Distrofina / Dependovirus / Distrofia Muscular de Duchenne / Mioblastos / Vetores Genéticos / Distrofia Muscular Animal Idioma: En Ano de publicação: 2020 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Terapia Genética / Distrofina / Dependovirus / Distrofia Muscular de Duchenne / Mioblastos / Vetores Genéticos / Distrofia Muscular Animal Idioma: En Ano de publicação: 2020 Tipo de documento: Article