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Biomarkers for prediction of skeletal disease progression in mucopolysaccharidosis type I.
Lund, Troy C; Doherty, Terence M; Eisengart, Julie B; Freese, Rebecca L; Rudser, Kyle D; Fung, Ellen B; Miller, Bradley S; White, Klane K; Orchard, Paul J; Whitley, Chester B; Polgreen, Lynda E.
Afiliação
  • Lund TC; Department of Pediatrics University of Minnesota Minneapolis Minnesota USA.
  • Doherty TM; Department of Pediatrics The Lundquist Institute at Harbor-UCLA Medical Center Torrance California USA.
  • Eisengart JB; Department of Pediatrics University of Minnesota Minneapolis Minnesota USA.
  • Freese RL; Biostatistical Design and Analysis Center, Clinical and Translational Science Institute University of Minnesota Minneapolis Minnesota USA.
  • Rudser KD; School of Public Health, Division of Biostatistics University of Minnesota Minneapolis Minnesota USA.
  • Fung EB; Department of Hematology University of California, San Francisco Benioff Children's Hospital Oakland California USA.
  • Miller BS; Department of Pediatrics University of Minnesota Minneapolis Minnesota USA.
  • White KK; Department of Orthopaedics and Sports Medicine Seattle Children's Hospital Seattle Washington USA.
  • Orchard PJ; Department of Pediatrics University of Minnesota Minneapolis Minnesota USA.
  • Whitley CB; Department of Pediatrics University of Minnesota Minneapolis Minnesota USA.
  • Polgreen LE; Department of Pediatrics The Lundquist Institute at Harbor-UCLA Medical Center Torrance California USA.
JIMD Rep ; 58(1): 89-99, 2021 Mar.
Article em En | MEDLINE | ID: mdl-33728251

Texto completo: 1 Base de dados: MEDLINE Idioma: En Ano de publicação: 2021 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Idioma: En Ano de publicação: 2021 Tipo de documento: Article