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A novel sustained-release cysteamine bitartrate formulation for the treatment of cystinosis: Pharmacokinetics and safety in healthy male volunteers.
Berends, Cécile L; Pagan, Lisa; van Esdonk, Michiel J; Klarenbeek, Naomi B; Bergmann, Kirsten R; Moerland, Matthijs; van der Wel, Vincent; de Visser, Saco J; Büller, Hans; de Loos, Frans; de Vries, Wouter S; Waals, Hans; de Leede, Leo G J; Burggraaf, Jacobus; Kamerling, Ingrid M C.
Afiliação
  • Berends CL; Centre for Human Drug Research (CHDR), Leiden, The Netherlands.
  • Pagan L; Leiden University Medical Center, Leiden, The Netherlands.
  • van Esdonk MJ; Centre for Human Drug Research (CHDR), Leiden, The Netherlands.
  • Klarenbeek NB; Leiden University Medical Center, Leiden, The Netherlands.
  • Bergmann KR; Centre for Human Drug Research (CHDR), Leiden, The Netherlands.
  • Moerland M; Centre for Human Drug Research (CHDR), Leiden, The Netherlands.
  • van der Wel V; Leiden University Medical Center, Leiden, The Netherlands.
  • de Visser SJ; Centre for Human Drug Research (CHDR), Leiden, The Netherlands.
  • Büller H; Centre for Human Drug Research (CHDR), Leiden, The Netherlands.
  • de Loos F; Leiden University Medical Center, Leiden, The Netherlands.
  • de Vries WS; Patient One, Leiden, The Netherlands.
  • Waals H; ZonMW, Den Haag, The Netherlands.
  • de Leede LGJ; Fair Medicine, Amsterdam, The Netherlands.
  • Burggraaf J; Fair Medicine, Amsterdam, The Netherlands.
  • Kamerling IMC; TioFarma, Oud-Beijerland, The Netherlands.
Pharmacol Res Perspect ; 9(2): e00739, 2021 04.
Article em En | MEDLINE | ID: mdl-33764642

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Cisteamina / Cistinose / Eliminadores de Cistina Idioma: En Ano de publicação: 2021 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Cisteamina / Cistinose / Eliminadores de Cistina Idioma: En Ano de publicação: 2021 Tipo de documento: Article