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Quality of life outcomes in two phase 3 trials of setmelanotide in patients with obesity due to LEPR or POMC deficiency.
Kühnen, Peter; Wabitsch, Martin; von Schnurbein, Julia; Chirila, Costel; Mallya, Usha G; Callahan, Patrick; Gnanasakthy, Ari; Poitou, Christine; Krabusch, Philipp M; Stewart, Murray; Clément, Karine.
Afiliação
  • Kühnen P; Charité - Universitätsmedizin Berlin, Corporate Member of Freie Universität Berlin und Humboldt-Universität zu Berlin, Institute for Experimental Pediatric Endocrinology, CVK, Augustenburger Platz 1, 13353, Berlin, Germany.
  • Wabitsch M; Division of Pediatric Endocrinology and Diabetes, Center for Rare Endocrine Diseases, Department of Pediatrics and Adolescent Medicine, University of Ulm, Eythstraße 24, 89075, Ulm, Germany.
  • von Schnurbein J; Division of Pediatric Endocrinology and Diabetes, Center for Rare Endocrine Diseases, Department of Pediatrics and Adolescent Medicine, University of Ulm, Eythstraße 24, 89075, Ulm, Germany.
  • Chirila C; RTI Health Solutions, 3040 East Cornwallis Road, P.O. Box 12194, Research Triangle Park, NC, 27709-2194, USA.
  • Mallya UG; Rhythm Pharmaceuticals, Inc., 222 Berkeley Street, Suite 1200, Boston, MA, 02116, USA.
  • Callahan P; Genesis Research, 111 River Street, Suite 1120, Hoboken, NJ, 07030, USA.
  • Gnanasakthy A; RTI Health Solutions, 3040 East Cornwallis Road, P.O. Box 12194, Research Triangle Park, NC, 27709-2194, USA.
  • Poitou C; Nutrition Department, Assistance Publique Hôpitaux de Paris, Pitié-Salpêtrière Hospital, IE3M Building, Room 637, 6th floor, 91 boulevard de l'Hôpital, 75013, Paris, France.
  • Krabusch PM; INSERM, Nutrition and Obesity; Systemic Approaches (NutriOmique) Research Group, Sorbonne University, Room 637, 6th floor, 91 boulevard de l'Hôpital, 75013, Paris, France.
  • Stewart M; Charité - Universitätsmedizin Berlin, Corporate Member of Freie Universität Berlin und Humboldt-Universität zu Berlin, Institute for Experimental Pediatric Endocrinology, CVK, Augustenburger Platz 1, 13353, Berlin, Germany.
  • Clément K; Rhythm Pharmaceuticals, Inc., 222 Berkeley Street, Suite 1200, Boston, MA, 02116, USA.
Orphanet J Rare Dis ; 17(1): 38, 2022 02 05.
Article em En | MEDLINE | ID: mdl-35123544

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Qualidade de Vida / Pró-Opiomelanocortina Idioma: En Ano de publicação: 2022 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Qualidade de Vida / Pró-Opiomelanocortina Idioma: En Ano de publicação: 2022 Tipo de documento: Article