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Efficacy and Safety of Fenfluramine for the Treatment of Seizures Associated With Lennox-Gastaut Syndrome: A Randomized Clinical Trial.
Knupp, Kelly G; Scheffer, Ingrid E; Ceulemans, Berten; Sullivan, Joseph E; Nickels, Katherine C; Lagae, Lieven; Guerrini, Renzo; Zuberi, Sameer M; Nabbout, Rima; Riney, Kate; Shore, Svetlana; Agarwal, Anupam; Lock, Michael; Farfel, Gail M; Galer, Bradley S; Gammaitoni, Arnold R; Davis, Ronald; Gil-Nagel, Antonio.
Afiliação
  • Knupp KG; Department of Neurology, Children's Hospital Colorado, Aurora.
  • Scheffer IE; Austin Hospital and Royal Children's Hospital, University of Melbourne, Melbourne, Victoria, Australia.
  • Ceulemans B; Department of Paediatric Neurology, Antwerp University Hospital, Antwerp, Belgium.
  • Sullivan JE; Weill Institute for Neurosciences, Benioff Children's Hospital, University of California San Francisco, San Francisco.
  • Nickels KC; Department of Neurology, Mayo Clinic, Rochester, Minnesota.
  • Lagae L; Steering Committee, European Reference Network EpiCARE, Lyon, France.
  • Guerrini R; Department of Paediatric Neurology, KU Leuven, Leuven, Belgium.
  • Zuberi SM; Pediatric Neurology and Neurogenetics Unit, Anna Meyer Children's Hospital, University of Florence, Florence, Italy.
  • Nabbout R; Neurobiologia e Neurogenetica dei Disturbi del Neurosviluppo, Istituto di Ricovero e Cura a Carattere Scientifico (IRCCS), Fondazione Stella Maris, Pisa, Italy.
  • Riney K; Paediatric Neurosciences Research Group, Royal Hospital for Children, Glasgow, United Kingdom.
  • Shore S; Department of Pediatric Neurology, Reference Centre for Rare Epilepsies, Necker-Enfants Malades Hospital, Imagine Institute, University Paris Descartes, Paris, France.
  • Agarwal A; Neuroscience Unit, Queensland Children's Hospital, South Brisbane, Queensland, Australia.
  • Lock M; School of Clinical Medicine, University of Queensland, St Lucia, Queensland, Australia.
  • Farfel GM; Zogenix Inc, Emeryville, California.
  • Galer BS; Now with Neurocrine Biosciences, San Diego, California.
  • Gammaitoni AR; Zogenix Inc, Emeryville, California.
  • Davis R; Zogenix Inc, Emeryville, California.
  • Gil-Nagel A; Now with Zogenix Inc, Haiku, Hawaii.
JAMA Neurol ; 79(6): 554-564, 2022 06 01.
Article em En | MEDLINE | ID: mdl-35499850

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Síndrome de Lennox-Gastaut Idioma: En Ano de publicação: 2022 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Assunto principal: Síndrome de Lennox-Gastaut Idioma: En Ano de publicação: 2022 Tipo de documento: Article