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Italian Real-Life Experience of Patients with Hereditary Transthyretin Amyloidosis Treated with Patisiran.
Di Stefano, Vincenzo; Fava, Antonella; Gentile, Luca; Guaraldi, Pietro; Leonardi, Luca; Poli, Loris; Tagliapietra, Matteo; Vastola, Michele; Fanara, Salvatore; Ferrero, Bruno; Giorgi, Mauro; Perfetto, Federico; Russo, Massimo; Russo, Domitilla.
Afiliação
  • Di Stefano V; Department of Biomedicine, Neuroscience and Advanced Diagnostic (BIND), University of Palermo, Palermo, Italy.
  • Fava A; Division of Cardiology, Heart Vascular and Thoracic Department, Città della Salute e della Scienza (Molinette Hospital- University of Turin), Turin, Italy.
  • Gentile L; Unit of Neurology and Neuromuscular Disease, Department of Clinical and Experimental Medicine, University of Messina, Messina, Italy.
  • Guaraldi P; IRCCS Istituto delle Scienze Neurologiche di Bologna, Bologna, Italy.
  • Leonardi L; Department of Neuroscience, Mental Health and Sensory Organs (NESMOS), Sapienza University of Rome Sant'Andrea Hospital, Rome, Italy.
  • Poli L; Department of Neurology, ASST Spedali Civili, Brescia, Italy.
  • Tagliapietra M; Department of Neurosciences, Biomedicine and Movement Sciences, University of Verona, Verona, Italy.
  • Vastola M; Tuscan Regional Amyloidosis Centre, Careggi University Hospital, Florence, Italy.
  • Fanara S; Neurosciences Department, Florence University, Rome, Italy.
  • Ferrero B; Department of Biomedicine, Neuroscience and Advanced Diagnostic (BIND), University of Palermo, Palermo, Italy.
  • Giorgi M; SC Neurology 2U, Department of Neuroscience "Rita Levi Montalcini", Città della Salute e della Scienza (Molinette Hospital -University of Turin), Turin, Italy.
  • Perfetto F; Division of Cardiology, Heart Vascular and Thoracic Department, Città della Salute e della Scienza (Molinette Hospital- University of Turin), Turin, Italy.
  • Russo M; Tuscan Regional Amyloidosis Centre, Careggi University Hospital, Florence, Italy.
  • Russo D; Unit of Neurology and Neuromuscular Disease, Department of Clinical and Experimental Medicine, University of Messina, Messina, Italy.
Pharmgenomics Pers Med ; 15: 499-514, 2022.
Article em En | MEDLINE | ID: mdl-35592550

Texto completo: 1 Base de dados: MEDLINE Idioma: En Ano de publicação: 2022 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Idioma: En Ano de publicação: 2022 Tipo de documento: Article