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Application of in-vitro-cultured primary hepatocytes to evaluate species translatability and AAV transduction mechanisms of action.
Liu, Su; Razon, Lisa; Ritchie, Olivia; Sihn, Choong-Ryoul; Handyside, Britta; Berguig, Geoffrey; Woloszynek, Jill; Zhang, Lening; Batty, Paul; Lillicrap, David; Agrawal, Vishal; Cortesio, Christa; Gebretsadik, Kahsay; Akeefe, Hassibullah; Colosi, Peter; Kim, Benjamin; Bunting, Stuart; Fong, Sylvia.
Afiliação
  • Liu S; Biology Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Razon L; Biology Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Ritchie O; Biology Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Sihn CR; Biology Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Handyside B; Biology Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Berguig G; Biology Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Woloszynek J; Biology Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Zhang L; Biology Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Batty P; Department of Pathology and Molecular Medicine, Richardson Laboratory, Queen's University, Kingston, ON K7L 3N6, Canada.
  • Lillicrap D; Department of Pathology and Molecular Medicine, Richardson Laboratory, Queen's University, Kingston, ON K7L 3N6, Canada.
  • Agrawal V; Biology Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Cortesio C; Biology Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Gebretsadik K; Biology Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Akeefe H; Biology Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Colosi P; Biology Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Kim B; Clinical Sciences, BioMarin Pharmaceutical, Inc., Novato, CA 94949, USA.
  • Bunting S; Biology Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
  • Fong S; Biology Research, BioMarin Pharmaceutical Inc., 105 Digital Drive, Novato, CA 94949, USA.
Mol Ther Methods Clin Dev ; 26: 61-71, 2022 Sep 08.
Article em En | MEDLINE | ID: mdl-35782594

Texto completo: 1 Base de dados: MEDLINE Idioma: En Ano de publicação: 2022 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Idioma: En Ano de publicação: 2022 Tipo de documento: Article