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Author Correction: Long-term safety and efficacy of lentiviral hematopoietic stem/progenitor cell gene therapy for Wiskott-Aldrich syndrome.
Magnani, A; Semeraro, M; Adam, F; Booth, C; Dupré, L; Morris, E C; Gabrion, A; Roudaut, C; Borgel, D; Toubert, A; Clave, E; Abdo, C; Gorochov, G; Petermann, R; Guiot, M; Miyara, M; Moshous, D; Magrin, E; Denis, A; Suarez, F; Lagresle, C; Roche, A M; Everett, J; Trinquand, A; Guisset, M; Bayford, J Xu; Hacein-Bey-Abina, S; Kauskot, A; Elfeky, R; Rivat, C; Abbas, S; Gaspar, H B; Macintyre, E; Picard, C; Bushman, F D; Galy, A; Fischer, A; Six, E; Thrasher, A J; Cavazzana, M.
Afiliação
  • Magnani A; Department of Biotherapy, Hôpital Universitaire Necker-Enfants Malades, Groupe Hospitalier Paris Centre, Assistance Publique-Hôpitaux de Paris, Paris, France.
  • Semeraro M; Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Paris Centre, Assistance Publique-Hôpitaux de Paris, INSERM CIC 1416, Paris, France.
  • Adam F; Clinical Investigation Center CIC 1419, Hôpital Universitaire Necker-Enfants Malades, Groupe Hospitalier Paris Centre, Université de Paris, Assistance Publique-Hôpitaux de Paris, Paris, France.
  • Booth C; INSERM, UMR_S1176, Université Paris-Saclay, Le Kremlin-Bicêtre, France.
  • Dupré L; Department of Paediatric Immunology, Great Ormond Street Hospital, London, UK.
  • Morris EC; Molecular and Cellular Immunology Section, UCL Great Ormond Street Institute of Child Health, London, UK.
  • Gabrion A; Toulouse Institute for Infectious and Inflammatory Diseases (INFINITy), INSERM, CNRS, Toulouse III Paul Sabatier University, Toulouse, France.
  • Roudaut C; Ludwig Boltzmann Institute for Rare and Undiagnosed Diseases, Vienna, Austria.
  • Borgel D; Department of Dermatology, Medical University of Vienna, Vienna, Austria.
  • Toubert A; Institute of Immunity and Transplantation, University College London, London, UK.
  • Clave E; Department of Immunology, Royal Free London Hospitals NHS Foundation Trust, London, UK.
  • Abdo C; Department of Biotherapy, Hôpital Universitaire Necker-Enfants Malades, Groupe Hospitalier Paris Centre, Assistance Publique-Hôpitaux de Paris, Paris, France.
  • Gorochov G; Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Paris Centre, Assistance Publique-Hôpitaux de Paris, INSERM CIC 1416, Paris, France.
  • Petermann R; Department of Biotherapy, Hôpital Universitaire Necker-Enfants Malades, Groupe Hospitalier Paris Centre, Assistance Publique-Hôpitaux de Paris, Paris, France.
  • Guiot M; Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Paris Centre, Assistance Publique-Hôpitaux de Paris, INSERM CIC 1416, Paris, France.
  • Miyara M; INSERM, UMR_S1176, Université Paris-Saclay, Le Kremlin-Bicêtre, France.
  • Moshous D; Laboratoire d'Hématologie, Assistance Publique-Hôpitaux de Paris, Hôpital Necker-Enfants Malades, Paris, France.
  • Magrin E; EMiLy, INSERM U1160, Institut de Recherche Saint Louis, Université de Paris, Paris, France.
  • Denis A; Laboratoire d'Immunologie et d'Histocompatibilité, Hôpital Saint-Louis, Assistance Publique-Hôpitaux de Paris, Paris, France.
  • Suarez F; EMiLy, INSERM U1160, Institut de Recherche Saint Louis, Université de Paris, Paris, France.
  • Lagresle C; Institut Necker-Enfants Malades (INEM), INSERM U1151, Université Paris Descartes Sorbonne Cité, Paris, France.
  • Roche AM; Laboratory of Onco-Hematology, Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades University Hospital, Paris, France.
  • Everett J; Département d'Immunologie, Groupement Hospitalier Pitié-Salpêtrière, Assistance Publique-Hôpitaux de Paris, Paris, France.
  • Trinquand A; Centre d'Immunologie et des Maladies Infectieuses-Paris (CIMI-Paris), INSERM, Sorbonne Université, Paris, France.
  • Guisset M; Platelet Immunology Department, INTS, Paris, France.
  • Bayford JX; Department of Biotherapy, Hôpital Universitaire Necker-Enfants Malades, Groupe Hospitalier Paris Centre, Assistance Publique-Hôpitaux de Paris, Paris, France.
  • Hacein-Bey-Abina S; Département d'Immunologie, Groupement Hospitalier Pitié-Salpêtrière, Assistance Publique-Hôpitaux de Paris, Paris, France.
  • Kauskot A; Centre d'Immunologie et des Maladies Infectieuses-Paris (CIMI-Paris), INSERM, Sorbonne Université, Paris, France.
  • Elfeky R; Department of Pediatric Immunology, Hematology and Rheumatology, Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades University Hospital, Paris, France.
  • Rivat C; Imagine Institute, Université Paris Centre, Paris, France.
  • Abbas S; Department of Biotherapy, Hôpital Universitaire Necker-Enfants Malades, Groupe Hospitalier Paris Centre, Assistance Publique-Hôpitaux de Paris, Paris, France.
  • Gaspar HB; Biotherapy Clinical Investigation Center, Groupe Hospitalier Universitaire Paris Centre, Assistance Publique-Hôpitaux de Paris, INSERM CIC 1416, Paris, France.
  • Macintyre E; Human Lymphohematopoiesis Laboratory, Imagine Institute, INSERM UMR 1163, Université de Paris, Paris, France.
  • Picard C; Imagine Institute, Université Paris Centre, Paris, France.
  • Bushman FD; Service d'Hématologie Adultes, Hôpital Necker-Enfants Malades, Assistance Publique-Hôpitaux de Paris, Centre Université de Paris, Paris, France.
  • Galy A; Human Lymphohematopoiesis Laboratory, Imagine Institute, INSERM UMR 1163, Université de Paris, Paris, France.
  • Fischer A; Department of Microbiology, University of Pennsylvania School of Medicine, Philadelphia, PA, USA.
  • Six E; Department of Microbiology, University of Pennsylvania School of Medicine, Philadelphia, PA, USA.
  • Thrasher AJ; Institut Necker-Enfants Malades (INEM), INSERM U1151, Université Paris Descartes Sorbonne Cité, Paris, France.
  • Cavazzana M; Laboratory of Onco-Hematology, Assistance Publique-Hôpitaux de Paris, Necker-Enfants Malades University Hospital, Paris, France.
Nat Med ; 28(10): 2217, 2022 Oct.
Article em En | MEDLINE | ID: mdl-35945284

Texto completo: 1 Base de dados: MEDLINE Idioma: En Ano de publicação: 2022 Tipo de documento: Article

Texto completo: 1 Base de dados: MEDLINE Idioma: En Ano de publicação: 2022 Tipo de documento: Article